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TITLE: Precision medicine for rare diseases: The times they are A-Changin'
AUTHORS: Amaral, Margarida D. ;
PUBLISHED: 2022, SOURCE: CURRENT OPINION IN PHARMACOLOGY, VOLUME: 63
INDEXED IN: Scopus WOS CrossRef: 7
12
TITLE: Using the genome to correct the ion transport defect in cystic fibrosis
AUTHORS: Amaral, Margarida D. ;
PUBLISHED: 2022, SOURCE: JOURNAL OF PHYSIOLOGY-LONDON, VOLUME: 601, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef: 1
13
TITLE: How to determine the mechanism of action of CFTR modulator compounds: A gateway to theranostics
AUTHORS: Amaral, MD ;
PUBLISHED: 2021, SOURCE: EUROPEAN JOURNAL OF MEDICINAL CHEMISTRY, VOLUME: 210
INDEXED IN: Scopus WOS CrossRef: 8
14
TITLE: A central role of the endoplasmic reticulum in the cell emerges from its functional contact sites with multiple organelles
AUTHORS: Almeida, C; Amaral, MD ;
PUBLISHED: 2020, SOURCE: CELLULAR AND MOLECULAR LIFE SCIENCES, VOLUME: 77, ISSUE: 23
INDEXED IN: Scopus WOS CrossRef: 17
15
TITLE: Activating alternative chloride channels to treat CF: Friends or Foes?
AUTHORS: Margarida D Amaral ; Jeffrey M Beekman;
PUBLISHED: 2020, SOURCE: Journal of Cystic Fibrosis, VOLUME: 19, ISSUE: 1
INDEXED IN: CrossRef: 6
16
TITLE: Activating alternative chloride channels to treat CF: Friends or Foes? Report on the Meeting of the Basic Science Working Group in Dubrovnik, Croatia
AUTHORS: Amaral, MD ; Beekman, JM;
PUBLISHED: 2020, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 19, ISSUE: 1
INDEXED IN: Scopus WOS
17
TITLE: CFTR processing, trafficking and interactions  Full Text
AUTHORS: Amaral, MD ; Hutt, DM; Tomati, V; Botelho, HM ; Pedemonte, N;
PUBLISHED: 2020, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 19
INDEXED IN: Scopus WOS CrossRef: 18
18
TITLE: Mutant CFTR Drives TWIST1 mediated epithelial-mesenchymal transition
AUTHORS: Quaresma, MC ; Pankonien, I; Clarke, LA ; Sousa, LS; Silva, IAL; Railean, V; Dousova, T; Fuxe, J; Amaral, MD;
PUBLISHED: 2020, SOURCE: CELL DEATH & DISEASE, VOLUME: 11, ISSUE: 10
INDEXED IN: Scopus WOS CrossRef: 32
19
TITLE: What Role Does CFTR Play in Development, Differentiation, Regeneration and Cancer?
AUTHORS: Amaral, MD ; Quaresma, MC; Pankonien, I;
PUBLISHED: 2020, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 21, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef: 43
20
TITLE: CFTR modulator theratyping: Current status, gaps and future directions
AUTHORS: Clancy, JP; Cotton, CU; Donaldson, SH; Solomon, GM; VanDevanter, DR; Boyle, MP; Gentzsch, M; Nick, JA; Illek, B; Wallenburg, JC; Sorscher, EJ; Amaral, MD ; Beekman, JM; Naren, AP; Bridges, RJ; Thomas, PJ; Cutting, G; Rowe, S; Durmowicz, AG; Mense, M; Boeck, KD; Skach, W; Penland, C; Joseloff, E; Bihler, H; Mahoney, J; Borowitz, D; Tuggle, KL; ...More
PUBLISHED: 2019, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 18, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef: 207
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