51
TITLE: Increased efficacy of VX-809 in different cellular systems results from an early stabilization effect of F508del-CFTR
AUTHORS: Farinha, CM; Sousa, M; Canato, S; Schmidt, A; Uliyakina, I; Amaral, MD ;
PUBLISHED: 2015, SOURCE: PHARMACOLOGY RESEARCH & PERSPECTIVES, VOLUME: 3, ISSUE: 4
INDEXED IN: Scopus WOS CrossRef Handle
53
TITLE: New pharmacological approaches for cystic fibrosis: Promises, progress, pitfalls  Full Text
AUTHORS: Scott C Bell; Kris De Boeck; Margarida D Amaral ;
PUBLISHED: 2015, SOURCE: PHARMACOLOGY & THERAPEUTICS, VOLUME: 145
INDEXED IN: Scopus WOS CrossRef
54
TITLE: Novel personalized therapies for cystic fibrosis: treating the basic defect in all patients  Full Text
AUTHORS: Amaral, MD ;
PUBLISHED: 2015, SOURCE: JOURNAL OF INTERNAL MEDICINE, VOLUME: 277, ISSUE: 2
INDEXED IN: Scopus WOS CrossRef
55
TITLE: Pharmacological evaluation of hybrid thiazolidin-4-one-1,3,5-triazines for NF-kappa B, biofilm and CFTR activity
AUTHORS: Jitendra Kumar Srivastava; Nikhil T Awatade; Hans Raj Bhat; Arthur Kmit; Karina Mendes; Margarida Ramos; Margarida D Amaral ; Udaya Pratap Singh;
PUBLISHED: 2015, SOURCE: RSC ADVANCES, VOLUME: 5, ISSUE: 108
INDEXED IN: Scopus WOS CrossRef
58
TITLE: Assessing the residual CFTR gene expression in human nasal epithelium cells bearing CFTR splicing mutations causing cystic fibrosis
AUTHORS: Laia Masvidal; Susana Igreja; Maria D Ramos; Antoni Alvarez; Javier De Gracia; Anabela Ramalho; Margarida D Amaral ; Sara Larriba; Teresa Casals;
PUBLISHED: 2014, SOURCE: European Journal of Human Genetics, VOLUME: 22, ISSUE: 6
INDEXED IN: Scopus
59
TITLE: Assessing the residual CFTR gene expression in human nasal epithelium cells bearing CFTR splicing mutations causing cystic fibrosis  Full Text
AUTHORS: Laia Masvidal; Susana Igreja; Maria D Ramos; Antoni Alvarez; Javier de Gracia; Anabela Ramalho ; Margarida D Amaral ; Sara Larriba; Teresa Casals;
PUBLISHED: 2014, SOURCE: EUROPEAN JOURNAL OF HUMAN GENETICS, VOLUME: 22, ISSUE: 6
INDEXED IN: Scopus WOS CrossRef
60
TITLE: CFTR functional measurements in human models for diagnosis, prognosis and personalized therapy: Report on the pre-conference meeting to the 11th ECFS Basic Science Conference, Malta, 26-29 March 2014  Full Text
AUTHORS: Jeffrey M Beekman; Isabelle Sermet Gaudelus; Kris de Boeck; Tanja Gonska; Nico Derichs; Marcus A Mall; Anil Mehta; Ulrich Martin; Mitch Drumm; Margarida D Amaral ;
PUBLISHED: 2014, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 13, ISSUE: 4
INDEXED IN: Scopus WOS
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