81
TITLE: Rapid progression of familial amyloidotic polyneuropathy A multinational natural history study
AUTHORS: David Adams; Teresa Coelho; Laura Obici; Giampaolo Merlini; Zoia Mincheva; Narupat Suanprasert; Brian R Bettencourt; Jared A Gollob; Pritesh J Gandhi; William J Litchy; Peter J Dyck;
PUBLISHED: 2015, SOURCE: NEUROLOGY, VOLUME: 85, ISSUE: 8
INDEXED IN: Scopus WOS CrossRef
82
TITLE: Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study  Full Text
AUTHORS: Ole B Suhr; Teresa Coelho; Juan Buades; Jean Pouget; Isabel Conceicao; John Berk; Hartmut Schmidt; Marcia Waddington Cruz; Josep M Campistol; Brian R Bettencourt; Akshay Vaishnaw; Jared Gollob; David Adams;
PUBLISHED: 2015, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 10, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
83
TITLE: PHASE 2 OPEN-LABEL EXTENSION STUDY (OLE) OF PATISIRAN, AN INVESTIGATIONAL siRNA INVESTIGATIONAL AGENT FOR FAMILIAL AMYLOID POLYNEUROPATHY (FAP)  Full Text
AUTHORS: Coelho, T; Suhr, O; Conceicao, I; Waddington Cruz, M; Schmidt, H; Buades, J; Campistol, J; Pouget, J; Berk, J; Falzone, R; White, L; Bettencourt, B; Cehelsky, J; Nochur, S; Vaishnaw, A; Gollob, J; Adams, D;
PUBLISHED: 2015, SOURCE: Biennial Meeting of the Peripheral-Nerve-Society in JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 20, ISSUE: 2
INDEXED IN: WOS
84
TITLE: Current status of ISIS-TTRRx phase 3 study in patients with transthyretin familial amyloid polyneuropathy (FAP)  Full Text
AUTHORS: Coelho, T; Martins M Silva; Ackermann, E; Yamashita, MM; Hughes, S; Monia, B;
PUBLISHED: 2015, SOURCE: 1st Congress of the European-Academy-of-Neurology in EUROPEAN JOURNAL OF NEUROLOGY, VOLUME: 22
INDEXED IN: WOS
85
TITLE: Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis  Full Text
AUTHORS: Morie A Gertz; Merrill D Benson; Peter J Dyck; Martha Grogan; Terresa Coelho; Marcia Cruz; John L Berk; Violaine Plante Bordeneuve; Hartmut H J Schmidt; Giampaolo Merlini;
PUBLISHED: 2015, SOURCE: JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, VOLUME: 66, ISSUE: 21
INDEXED IN: WOS CrossRef
86
TITLE: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTHORS: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLISHED: 2015, SOURCE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, ISSUE: 11
INDEXED IN: WOS CrossRef
87
TITLE: A cerebral abscess at first internist glance
AUTHORS: Ribeiro, R; Patrício, C; Coelho, MMV; Brotas, V;
PUBLISHED: 2015, SOURCE: BMJ Case Reports, VOLUME: 2015
INDEXED IN: Scopus CrossRef
89
TITLE: Familial Amyloid Polyneuropathy treatment with Tafamidis - evaluation of one- and two-year treatment in Porto, Portugal  Full Text
AUTHORS: Coelho, T; Da Silva, AM; Alves, C; Cardoso, M; Monteiro, C; Fonseca, I ; Rodrigues, C; Costa, V;
PUBLISHED: 2015, SOURCE: Orphanet Journal of Rare Diseases, VOLUME: 10, ISSUE: Suppl 1
INDEXED IN: Scopus CrossRef: 2
90
TITLE: Overcoming artefact: anticipation in 284 Portuguese kindreds with familial amyloid polyneuropathy (FAP) ATTRV30M
AUTHORS: Lemos, C ; Coelho, T; Alves Ferreira, M; Martins da Silva, A; Sequeiros, J ; Mendonca, D ; Sousa, A ;
PUBLISHED: 2014, SOURCE: JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 85, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef: 48
Page 9 of 12. Total results: 113.