Rui Jorge Gonçalves Pereira Nobre
AuthID: R-000-FW0
1
TITLE: A systematic screening assay identifies efficient small guide RNAs for CRISPR activation
AUTHORS: Arvidsson, Elin; Lobo, Diana Duarte; Sabarese, Ermelinda; Duarte, Fabio; Nobre, Rui Jorge; Quintino, Luis; Lundberg, Cecilia;
PUBLISHED: 2025, SOURCE: FRONTIERS IN BIOENGINEERING AND BIOTECHNOLOGY, VOLUME: 13
AUTHORS: Arvidsson, Elin; Lobo, Diana Duarte; Sabarese, Ermelinda; Duarte, Fabio; Nobre, Rui Jorge; Quintino, Luis; Lundberg, Cecilia;
PUBLISHED: 2025, SOURCE: FRONTIERS IN BIOENGINEERING AND BIOTECHNOLOGY, VOLUME: 13
2
TITLE: Gene Editing forATXN3Inactivation in Machado-Joseph disease: CRISPR-Cas9 as a Therapeutic Alternative to TALEN-Induced Toxicity
AUTHORS: Sara Monteiro Lopes; Miguel Monteiro Lopes; Daniela Oliveira; Magda Matos Santana; Ana Rita Fernandes; Ana Vasconcelos-Ferreira; Dina Pereira; Maria Casquinha; Clévio Nóbrega; Carlos A Matos; Neville E Sanjana; Patrick D Hsu; Fei Ann Ran; Lukasz Swiech; Le Cong; Feng Zhang; Rui Jorge Nobre; Luís Pereira de Almeida;
PUBLISHED: 2025
AUTHORS: Sara Monteiro Lopes; Miguel Monteiro Lopes; Daniela Oliveira; Magda Matos Santana; Ana Rita Fernandes; Ana Vasconcelos-Ferreira; Dina Pereira; Maria Casquinha; Clévio Nóbrega; Carlos A Matos; Neville E Sanjana; Patrick D Hsu; Fei Ann Ran; Lukasz Swiech; Le Cong; Feng Zhang; Rui Jorge Nobre; Luís Pereira de Almeida;
PUBLISHED: 2025
3
TITLE: A systematic screening assay identifies efficient small guide RNAs for CRISPR activation
AUTHORS: Elin Arvidsson; Diana Duarte Lobo; Ermelinda Sabarese; Fabio Duarte; Rui Jorge Nobre; Luis Quintino; Cecilia Lundberg;
PUBLISHED: 2025, SOURCE: Frontiers in Bioengineering and Biotechnology, VOLUME: 13
AUTHORS: Elin Arvidsson; Diana Duarte Lobo; Ermelinda Sabarese; Fabio Duarte; Rui Jorge Nobre; Luis Quintino; Cecilia Lundberg;
PUBLISHED: 2025, SOURCE: Frontiers in Bioengineering and Biotechnology, VOLUME: 13
4
TITLE: Spinocerebellar ataxia type 3: from pathogenesis to promising therapeutics Full Text
AUTHORS: Ana Carolina Silva; Miguel Monteiro Lopes; Diana Duarte Lobo; Carina Henriques; Luís Pereira de Almeida; Rui Jorge Nobre;
PUBLISHED: 2025, SOURCE: Trends in Molecular Medicine
AUTHORS: Ana Carolina Silva; Miguel Monteiro Lopes; Diana Duarte Lobo; Carina Henriques; Luís Pereira de Almeida; Rui Jorge Nobre;
PUBLISHED: 2025, SOURCE: Trends in Molecular Medicine
5
TITLE: Innate immunocompetent iNSpheroids: A hiPSC-derived 3D model to study the central nervous system captures an early CNS response to rAAV
AUTHORS: Catarina M Gomes; Gabriela Silva; Mafalda Aleixo; Daniel Simão; Stephan J Holtkamp; Diana D Lobo; Pradeep Harish; Rosalind Jenkins; Lek Dahal; Rui J Nobre; Luís P Almeida; Mark Trautwein; Paula M Alves; Catarina Brito;
PUBLISHED: 2025
AUTHORS: Catarina M Gomes; Gabriela Silva; Mafalda Aleixo; Daniel Simão; Stephan J Holtkamp; Diana D Lobo; Pradeep Harish; Rosalind Jenkins; Lek Dahal; Rui J Nobre; Luís P Almeida; Mark Trautwein; Paula M Alves; Catarina Brito;
PUBLISHED: 2025
6
TITLE: RNA-based liposomes for oral cancer: From biophysical characterization to biological evaluation Full Text
AUTHORS: Lopes Nunes, Jessica; Simo, Pedro; Moreira, David; Leandro, Kevin; Nobre, Rui Jorge; de Almeida, Luis Pereira ; Campello, Maria Paula Cabral; Oliveira, Maria Cristina; Paulo, Antonio; Coutinho, Ana; Melo, Ana M.; Tomaz, Candida; Cruz, Carla ;
PUBLISHED: 2024, SOURCE: INTERNATIONAL JOURNAL OF BIOLOGICAL MACROMOLECULES, VOLUME: 259
AUTHORS: Lopes Nunes, Jessica; Simo, Pedro; Moreira, David; Leandro, Kevin; Nobre, Rui Jorge; de Almeida, Luis Pereira ; Campello, Maria Paula Cabral; Oliveira, Maria Cristina; Paulo, Antonio; Coutinho, Ana; Melo, Ana M.; Tomaz, Candida; Cruz, Carla ;
PUBLISHED: 2024, SOURCE: INTERNATIONAL JOURNAL OF BIOLOGICAL MACROMOLECULES, VOLUME: 259
7
TITLE: Viral-based animal models in polyglutamine disorders
AUTHORS: Henriques, Carina; Lopes, Miguel M.; Silva, Ana C.; Lobo, Diana D.; Aron Badin, Romina; Hantraye, Philippe; Pereira de Almeida, Luis ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: BRAIN, VOLUME: 147, ISSUE: 4
AUTHORS: Henriques, Carina; Lopes, Miguel M.; Silva, Ana C.; Lobo, Diana D.; Aron Badin, Romina; Hantraye, Philippe; Pereira de Almeida, Luis ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: BRAIN, VOLUME: 147, ISSUE: 4
8
TITLE: Isolation of Adeno-associated Viral Vectors Through a Single-step and Semi-automated Heparin Affinity Chromatography Protocol
AUTHORS: Lopes, Miguel M.; Lopes, Sara M.; Baganha, Rafael; Henriques, Carina; Silva, Ana C.; Lobo, Diana D.; Cortes, Luisa; de Almeida, Luis Pereira ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, VOLUME: 2024, ISSUE: 206
AUTHORS: Lopes, Miguel M.; Lopes, Sara M.; Baganha, Rafael; Henriques, Carina; Silva, Ana C.; Lobo, Diana D.; Cortes, Luisa; de Almeida, Luis Pereira ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, VOLUME: 2024, ISSUE: 206
9
TITLE: Molecular therapy for polyQ disorders: from bench to clinical trials
AUTHORS: João de Sousa Lourenço; Ana Silva; Luís Pereira de Almeida ; Rui Nobre;
PUBLISHED: 2024, SOURCE: Trends in Molecular Medicine
AUTHORS: João de Sousa Lourenço; Ana Silva; Luís Pereira de Almeida ; Rui Nobre;
PUBLISHED: 2024, SOURCE: Trends in Molecular Medicine
10
TITLE: Exploring the potential of cell-derived vesicles for transient delivery of gene editing payloads
AUTHORS: Leandro, Kevin; Rufino Ramos, David; Breyne, Koen; Di Ianni, Emilio; Lopes, Sara M.; Nobre, Rui Jorge; Kleinstiver, Benjamin P.; Perdiga, Pedro R. L.; Breakefield, Xandra O.; de Almeida, Luis Pereira ;
PUBLISHED: 2024, SOURCE: ADVANCED DRUG DELIVERY REVIEWS, VOLUME: 211
AUTHORS: Leandro, Kevin; Rufino Ramos, David; Breyne, Koen; Di Ianni, Emilio; Lopes, Sara M.; Nobre, Rui Jorge; Kleinstiver, Benjamin P.; Perdiga, Pedro R. L.; Breakefield, Xandra O.; de Almeida, Luis Pereira ;
PUBLISHED: 2024, SOURCE: ADVANCED DRUG DELIVERY REVIEWS, VOLUME: 211