Rui Jorge Gonçalves Pereira Nobre
AuthID: R-000-FW0
11
TITLE: rAAV-Delivered Bicistronic Artificial microRNAs for Allele-Specific Silencing Improve Motor and Molecular Outcomes in Spinocerebellar Ataxia Type 3
AUTHORS: Ana Carolina Silva; Carina Henriques; Diana D Lobo; Ana Rita Fernandes; Miguel M Lopes; Kevin Leandro; Dina Pereira; Sónia P Duarte; Sara M Lopes; Magda M Santana; Amal Dakka; Steve De Marco; Marla Weetall; Jana Narasimhan; Anu Bhattacharyya; Rui Jorge Nobre; Luís Pereira de Almeida ;
PUBLISHED: 2025
AUTHORS: Ana Carolina Silva; Carina Henriques; Diana D Lobo; Ana Rita Fernandes; Miguel M Lopes; Kevin Leandro; Dina Pereira; Sónia P Duarte; Sara M Lopes; Magda M Santana; Amal Dakka; Steve De Marco; Marla Weetall; Jana Narasimhan; Anu Bhattacharyya; Rui Jorge Nobre; Luís Pereira de Almeida ;
PUBLISHED: 2025
12
TITLE: AAV-mediated allele-specific silencing alleviates neuropathology in a novel non-human primate model of Spinocerebellar ataxia type 3
AUTHORS: Carina Henriques; Diana Duarte Lobo; Ana Carolina Silva; Ana Rita Fernandes; Miguel Monteiro Lopes; Audrey Fayard; Caroline Jan; Sophie Lecourtois; Martine Guillermier; Julien Flament; João Castelhano; Miguel Castelo-Branco; Rui Caetano Oliveira; Philippe Hantraye; Padmaja Yalamanchili; Steven de Marco; Romina Aron Badin; Luís Pereira de Almeida ; Rui Jorge Nobre;
PUBLISHED: 2025
AUTHORS: Carina Henriques; Diana Duarte Lobo; Ana Carolina Silva; Ana Rita Fernandes; Miguel Monteiro Lopes; Audrey Fayard; Caroline Jan; Sophie Lecourtois; Martine Guillermier; Julien Flament; João Castelhano; Miguel Castelo-Branco; Rui Caetano Oliveira; Philippe Hantraye; Padmaja Yalamanchili; Steven de Marco; Romina Aron Badin; Luís Pereira de Almeida ; Rui Jorge Nobre;
PUBLISHED: 2025
13
TITLE: RNA-based liposomes for oral cancer: From biophysical characterization to biological evaluation Full Text
AUTHORS: Lopes Nunes, Jessica; Simo, Pedro; Moreira, David; Leandro, Kevin; Nobre, Rui Jorge; de Almeida, Luis Pereira ; Campello, Maria Paula Cabral; Oliveira, Maria Cristina; Paulo, Antonio; Coutinho, Ana; Melo, Ana M.; Tomaz, Candida; Cruz, Carla ;
PUBLISHED: 2024, SOURCE: INTERNATIONAL JOURNAL OF BIOLOGICAL MACROMOLECULES, VOLUME: 259
AUTHORS: Lopes Nunes, Jessica; Simo, Pedro; Moreira, David; Leandro, Kevin; Nobre, Rui Jorge; de Almeida, Luis Pereira ; Campello, Maria Paula Cabral; Oliveira, Maria Cristina; Paulo, Antonio; Coutinho, Ana; Melo, Ana M.; Tomaz, Candida; Cruz, Carla ;
PUBLISHED: 2024, SOURCE: INTERNATIONAL JOURNAL OF BIOLOGICAL MACROMOLECULES, VOLUME: 259
14
TITLE: Viral-based animal models in polyglutamine disorders
AUTHORS: Henriques, Carina; Lopes, Miguel M.; Silva, Ana C.; Lobo, Diana D.; Aron Badin, Romina; Hantraye, Philippe; Pereira de Almeida, Luis ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: BRAIN, VOLUME: 147, ISSUE: 4
AUTHORS: Henriques, Carina; Lopes, Miguel M.; Silva, Ana C.; Lobo, Diana D.; Aron Badin, Romina; Hantraye, Philippe; Pereira de Almeida, Luis ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: BRAIN, VOLUME: 147, ISSUE: 4
15
TITLE: Isolation of Adeno-associated Viral Vectors Through a Single-step and Semi-automated Heparin Affinity Chromatography Protocol
AUTHORS: Lopes, Miguel M.; Lopes, Sara M.; Baganha, Rafael; Henriques, Carina; Silva, Ana C.; Lobo, Diana D.; Cortes, Luisa; de Almeida, Luis Pereira ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, VOLUME: 2024, ISSUE: 206
AUTHORS: Lopes, Miguel M.; Lopes, Sara M.; Baganha, Rafael; Henriques, Carina; Silva, Ana C.; Lobo, Diana D.; Cortes, Luisa; de Almeida, Luis Pereira ; Nobre, Rui Jorge;
PUBLISHED: 2024, SOURCE: JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, VOLUME: 2024, ISSUE: 206
16
TITLE: Molecular therapy for polyQ disorders: from bench to clinical trials
AUTHORS: João de Sousa Lourenço; Ana Silva; Luís Pereira de Almeida ; Rui Nobre;
PUBLISHED: 2024, SOURCE: Trends in Molecular Medicine
AUTHORS: João de Sousa Lourenço; Ana Silva; Luís Pereira de Almeida ; Rui Nobre;
PUBLISHED: 2024, SOURCE: Trends in Molecular Medicine
17
TITLE: Exploring the potential of cell-derived vesicles for transient delivery of gene editing payloads
AUTHORS: Leandro, Kevin; Rufino Ramos, David; Breyne, Koen; Di Ianni, Emilio; Lopes, Sara M.; Nobre, Rui Jorge; Kleinstiver, Benjamin P.; Perdiga, Pedro R. L.; Breakefield, Xandra O.; de Almeida, Luis Pereira ;
PUBLISHED: 2024, SOURCE: ADVANCED DRUG DELIVERY REVIEWS, VOLUME: 211
AUTHORS: Leandro, Kevin; Rufino Ramos, David; Breyne, Koen; Di Ianni, Emilio; Lopes, Sara M.; Nobre, Rui Jorge; Kleinstiver, Benjamin P.; Perdiga, Pedro R. L.; Breakefield, Xandra O.; de Almeida, Luis Pereira ;
PUBLISHED: 2024, SOURCE: ADVANCED DRUG DELIVERY REVIEWS, VOLUME: 211
18
TITLE: Small non-coding RNA content in plasma-derived extracellular vesicles distinguish ataxic SCA3 mutation carriers from pre-ataxic and control subjects
AUTHORS: Magda M Santana; Patrick Silva; Maria M Pinto; Laetitia Gaspar; Rui Nobre; Sónia Duarte; Tânia Monteiro Marques; Margarida Gama-Carvalho ; Cristina Januário; Inês Cunha; Joana Afonso Ribeiro; Jeannette Hübener-Schmid; Jon Infante; Mafalda Raposo; Manuela Lima ; Hector Garcia-Moreno; Paola Giunti; Bart van de Warrenburg; Matthis Synofzik; Jennifer Faber; ...More
PUBLISHED: 2024
AUTHORS: Magda M Santana; Patrick Silva; Maria M Pinto; Laetitia Gaspar; Rui Nobre; Sónia Duarte; Tânia Monteiro Marques; Margarida Gama-Carvalho ; Cristina Januário; Inês Cunha; Joana Afonso Ribeiro; Jeannette Hübener-Schmid; Jon Infante; Mafalda Raposo; Manuela Lima ; Hector Garcia-Moreno; Paola Giunti; Bart van de Warrenburg; Matthis Synofzik; Jennifer Faber; ...More
PUBLISHED: 2024
19
TITLE: Science around the world Full Text
AUTHORS: Griffiths, Meaghan J.; Nobre, Rui J.;
PUBLISHED: 2024, SOURCE: TRENDS IN MOLECULAR MEDICINE, VOLUME: 30, ISSUE: 9
AUTHORS: Griffiths, Meaghan J.; Nobre, Rui J.;
PUBLISHED: 2024, SOURCE: TRENDS IN MOLECULAR MEDICINE, VOLUME: 30, ISSUE: 9
20
TITLE: MiR-186-5p inhibition restores synaptic transmission and neuronal network activity in a model of chronic stress Full Text
AUTHORS: Rodrigues, Beatriz; Leitao, Ricardo A.; Santos, Monica; Trofimov, Alexander; Silva, Mariline; Inacio, angela S.; Abreu, Monica; Nobre, Rui J.; Costa, Jessica; Cardoso, Ana Luisa ; Milosevic, Ira; Peca, Joao; Oliveiros, Barbara; Pereira de Almeida, Luis ; Pinheiro, Paulo S.; Carvalho, Ana Luisa ;
PUBLISHED: 2024, SOURCE: MOLECULAR PSYCHIATRY
AUTHORS: Rodrigues, Beatriz; Leitao, Ricardo A.; Santos, Monica; Trofimov, Alexander; Silva, Mariline; Inacio, angela S.; Abreu, Monica; Nobre, Rui J.; Costa, Jessica; Cardoso, Ana Luisa ; Milosevic, Ira; Peca, Joao; Oliveiros, Barbara; Pereira de Almeida, Luis ; Pinheiro, Paulo S.; Carvalho, Ana Luisa ;
PUBLISHED: 2024, SOURCE: MOLECULAR PSYCHIATRY