21
TITLE: Differential Impact of Mutant Ataxin-3 Expression in Different Hindbrain Regions
AUTHORS: Carina Henriques; Marta Silva; Antonio Silva; David Rufino-Ramos; Miguel M Lopes; Romina Badin; Philippe Hantraye; Luis Pereira de Almeida; Rui Nobre;
PUBLISHED: 2024
INDEXED IN: CrossRef
IN MY: ORCID
22
TITLE: ALTERED TIGHT JUNCTION-ASSOCIATED PROTEINS SUBCELLULAR LOCALIZATION IN MACHADO-JOSEPH DISEASE/ SPINOCEREBELLAR ATAXIA TYPE 3  Full Text
AUTHORS: Barros, Ines; Gonzaga, Daniela; Lobo, Diana; Nobre, Rui Jorge; Martins, Ines; Silva, Antonio; Duarte, Sonia; De Almeida, Luis Pereira; Miranda, Catarina Oliveira ;
PUBLISHED: 2023, SOURCE: 26th Annual Meeting of the Portuguese-Society-of-Human-Genetics (SPGH) in MEDICINE, VOLUME: 102, ISSUE: 13
INDEXED IN: WOS
IN MY: ORCID
23
TITLE: MiR-186-5p inhibition restores synaptic transmission and neuronal network activity in a model of chronic stress
AUTHORS: Ana Luisa Carvalho; Beatriz Rodrigues; Ricardo Leitão; Mónica Santos; Alexander Trofimov; Mariline Silva; Ângela Inácio; Mónica Abreu; Rui Jorge Nobre; Jéssica Costa; Ana Luisa Cardoso; Ira Milosevic; João Peça; Luís Pereira de Almeida; Paulo Pinheiro;
PUBLISHED: 2023
INDEXED IN: CrossRef
IN MY: ORCID
24
TITLE: Isolation of Biologically Active Extracellular Vesicles-Associated AAVs for Gene Delivery to the Brain by Size Exclusion Chromatography
AUTHORS: Carina Henriques; Miguel M Lopes; Patrícia Albuquerque; David Rufino-Ramos; Laetitia S Gaspar; Diana Lobo; Kevin Leandro; Ana Carolina Silva; Rafael Baganha; Sónia Duarte; Casey A Maguire; Magda Santana; Luís Pereira de Almeida; Rui Jorge Nobre;
PUBLISHED: 2023
INDEXED IN: CrossRef
IN MY: ORCID
25
TITLE: Isolation of Biologically Active Extracellular Vesicles-Associated AAVs for Gene Delivery to the Brain by Size Exclusion Chromatography
AUTHORS: Luis Pereira de Almeida; Carina Henriques; Miguel Lopes; Patrícia Albuquerque; David Rufino Ramos; Laetitia Gaspar; Diana Lobo; Kevin Leandro; Ana Silva; Rafael Baganha; Sónia Duarte; Casey Maguire; Magda Santana; Rui Nobre;
PUBLISHED: 2023
INDEXED IN: CrossRef
IN MY: ORCID
26
TITLE: Liver injury in critically ill patients with COVID-19: a case series
AUTHORS: Filipe S Cardoso; Rui Pereira; Nuno Germano;
PUBLISHED: 2020, SOURCE: CRITICAL CARE, VOLUME: 24, ISSUE: 1
INDEXED IN: Scopus WOS
27
TITLE: Allele-Specific AAV-Based Silencing of Mutant Ataxin-3 Alleviates Neuropathology and Motor Deficits in Spinocerebellar Ataxia Type 3
AUTHORS: Rui Jorge Nobre; Joana Saraiva; Magda Santana; Clelia Fusco; Susana Paixao; Catarina Miranda ; Lorena Petrella; Jose Sereno; Joao Castelhano; Miguel Castelo Branco; Miguel Sena Esteves; Luis Pereira de Almeida;
PUBLISHED: 2020, SOURCE: 23rd Annual Meeting of the American-Society-for-Gene-and-Cell-Therapy in MOLECULAR THERAPY, VOLUME: 28, ISSUE: 4
INDEXED IN: WOS
IN MY: ORCID
28
TITLE: Repeated transplantation of mesenchymal stromal cells in Machado-Joseph disease/Spinocerebellar ataxia type-3 mice can sustainably alleviate phenotypic symptoms and ameliorations can be monitored through magnetic resonance spectroscopy  Full Text
AUTHORS: Catarina Oliveira Miranda ; Adriana Marcelo; Teresa Pereira Silva; Joao Barata; Ana Vasconcelos Ferreira; Dina Pereira; Sonia Duarte; Ines Barros; Clevio Nobrega; Jose Sereno; Lorena Petrella; Vitor Hugo Paiva; Joao Castelhano; Rui Jorge Nobre; Celia Gomes; Miguel Castelo Branco; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 49
INDEXED IN: WOS
IN MY: ORCID
30
TITLE: A miRNA-based gene therapy approach to knock-down mutant ATXN3: Alleviation of Machado-Joseph disease phenotype in two mouse models upon two routes of administration  Full Text
AUTHORS: Rui Jorge Nobre; Joana Saraiva; Clelia Fusco; Susana Paixao; Magda Santana; Catarina Miranda ; Lorena Petrella; Jose Sereno; Joao Castelhano; Miguel Castelo Branco; Miguel Sena Esteves; Luis Almeida;
PUBLISHED: 2019, SOURCE: EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 49
INDEXED IN: WOS
Page 3 of 5. Total results: 46.