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TITLE: Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy
AUTHORS: Adams, David; Wixner, Jonas; Polydefkis, Michael; Berk, John L.; Conceicao, Isabel M.; Dispenzieri, Angela; Peltier, Amanda; Ueda, Mitsuharu; Bender, Shaun; Capocelli, Kelley; Jay, Patrick Y.; Yureneva, Elena; Obici, Laura; Patisiran Global OLE Study Grp;
PUBLISHED: 2025, SOURCE: JAMA NEUROLOGY
INDEXED IN: Scopus WOS
2
TITLE: Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform (vol 271, pg 6655, 2024)  Full Text
AUTHORS: Conceicao, Isabel; Berk, John L.; Weiler, Markus; Kowacs, Pedro A.; Dasgupta, Noel R.; Khella, Sami; Chao, Chi Chao; Attarian, Shahram; Kwoh, T. Jesse; Jung, Shiangtung W.; Chen, Jersey; Viney, Nicholas J.; Yu, Rosie Z.; Gertz, Morie; Masri, Ahmad; Cruz, Marcia Waddington; Coelho, Teresa;
PUBLISHED: 2025, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 272, ISSUE: 2
INDEXED IN: WOS
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TITLE: Effect of Eplontersen on Cardiac Structure and Function in Patients With Hereditary Transthyretin Amyloidosis  Full Text
AUTHORS: Masri, Ahmad; Maurer, Mathew S.; Claggett, Brian L.; Kulac, Ian; Cruz, Marcia Waddington; Concei, Isabel; Weiler, Markus; Berk, John L.; Gertz, Morie; Gillmore, Julian D.; Rush, Stephen; Chen, Jersey; Zhou, Wunan; Kwoh, Jesse; Duran, Jason M.; Tsimikas, Sotirios; Solomon, Scott D.;
PUBLISHED: 2024, SOURCE: JOURNAL OF CARDIAC FAILURE, VOLUME: 30, ISSUE: 8
INDEXED IN: Scopus WOS
4
TITLE: Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform  Full Text
AUTHORS: Conceicao, Isabel; Berk, John L.; Weiler, Markus; Kowacs, Pedro A.; Dasgupta, Noel R.; Khella, Sami; Chao, Chi Chao; Attarian, Shahram; Kwoh, T. Jesse; Jung, Shiangtung W.; Chen, Jersey; Viney, Nicholas J.; Yu, Rosie Z.; Gertz, Morie; Masri, Ahmad; Cruz, Marcia Waddington; Coelho, Teresa;
PUBLISHED: 2024, SOURCE: JOURNAL OF NEUROLOGY
INDEXED IN: Scopus WOS
5
TITLE: NEUROPATHY IMPAIRMENT AND NUTRITIONAL STATUS WITH EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS  Full Text
AUTHORS: Conceicao, Isabel; Wixner, Jonas; Berk, John; Adams, David; Polydefkis, Michael; Attarian, Shahram; Gillmore, Julian; Dyck, P. James; Coelho, Teresa; Chen, Jersey; Hardy, Elise; Kwoh, Jesse; Natman, Jonatan; Cruz, Marcia Waddington;
PUBLISHED: 2024, SOURCE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 29
INDEXED IN: WOS
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TITLE: EPLONTERSEN IMPROVES AUTONOMIC NEUROPATHY SYMPTOMS IN HEREDITARY ATTR: AN ANALYSIS FROM NEURO-TTRANSFORM  Full Text
AUTHORS: Wixner, Jonas; Berk, John; Adams, David; Polydefkis, Michael; Conceicao, Isabel; Attarian, Shahram; Gillmore, Julian; Dyck, P. James; Folkvaljon, Folke; Zhou, Wunan; Chen, Jersey; Schneider, Eugene; Viney, Nicholas; Kwoh, Jesse; Coelho, Teresa; Cruz, Marcia Waddington;
PUBLISHED: 2024, SOURCE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 29
INDEXED IN: WOS
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TITLE: Effects of eplontersen on symptoms of autonomic neuropathy in hereditary transthyretin-mediated amyloidosis: secondary analysis from the NEURO-TTRansform trial  Full Text
AUTHORS: Wixner, Jonas; Berk, John L.; Adams, David; Polydefkis, Michael; Conceicao, Isabel; Attarian, Shahram; Gillmore, Julian D.; Dyck, P. James B.; Folkvaljon, Folke; Zhou, Wunan; Chen, Jersey; Viney, Nicholas J.; Kwoh, T. Jesse; Coelho, Teresa; Waddington Cruz, Marcia;
PUBLISHED: 2024, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
INDEXED IN: Scopus WOS
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TITLE: Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTHORS: Wixner, Jonas; Conceicao, Isabel; Berk, John; Adams, David; Polydefkis, Michael; Shahram, Attarian; Gillmore, Julian D.; Dyck, P. James B.; Coelho, Teresa; Chen, Jersey; Hardy, Elise; Kwoh, Jesse; Natman, Jonatan; Cruz, Marcia Waddington;
PUBLISHED: 2024, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, VOLUME: 31
INDEXED IN: WOS
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TITLE: Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy
AUTHORS: Coelho, Teresa; Marques, Wilson; Dasgupta, Noel R.; Chao, Chi Chao; Parman, Yesim; Franca, Marcondes Cavalcante; Guo, Yuh Cherng; Wixner, Jonas; Ro, Long Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington; Neuro ttransform Investigators; ...More
PUBLISHED: 2023, SOURCE: JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, VOLUME: 330, ISSUE: 15
INDEXED IN: Scopus WOS
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TITLE: HELIOS-A: STUDY OF VUTRISIRAN IN PATIENTS WITH HATTR AMYLOIDOSIS  Full Text
AUTHORS: Adams, David; Tournev, Ivailo L.; Taylor, Mark S.; Coelho, Teresa; Plante Bordeneuve, Violaine; Berk, John L.; Gonzalez Duarte, Alejandra; Gillmore, Julian D.; Low, Soon chai; Sekijima, Yoshiki; Obici, Laura; Chen, Chongshu; Badri, Prajakta; Arum, Seth; Vest, John; Polydefkis, Michael;
PUBLISHED: 2022, SOURCE: 12th Annual Meeting of the Italian-Association-for-the-Study-of-the-Peripheral-Nervous-System (ASNP) in JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 27
INDEXED IN: WOS
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