11
TITLE: HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy  Full Text
AUTHORS: Adams, D; Tournev, I; Taylor, M; Coelho, T; Plante Bordeneuve, V; Berk, J; Gonzalez Duarte, A; Gillmore, J; Low, SC; Sekijima, Y; Obici, L; Blakesley, R; Arum, S; Shilling, R; Vest, J; Polydefkis, M;
PUBLISHED: 2021, SOURCE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 26, ISSUE: 3
INDEXED IN: WOS
12
TITLE: Efficacy and safety with > 3 years of inotersen treatment for hereditary transthyretin amyloid polyneuropathy  Full Text
AUTHORS: Brannagan, T; Wang, A; Polydefkis, M; Dyck, P; Berk, J; Drachman, B; Gorevic, P; Coelho, T; Whelan, C; Conceicao, I; Plante Bordeneuve, V; Merlini, G; Obici, L; Schmidt, H; Plana, JMC; Gamez, J; Kristen, A; Mazzeo, A; Gentile, L; Narayana, A; Olugemo, K; Aquino, P; Benson, M; Gertz, M; ...More
PUBLISHED: 2021, SOURCE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 26, ISSUE: 3
INDEXED IN: WOS
13
TITLE: HELIOS-A: 9-month Results from the Phase 3 Study of Vutrisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
AUTHORS: Adams, D; Tournev, IL; Taylor, MS; Coelho, T; Plante Bordeneuve, V; Berk, JL; Gonzalez Duarte, A; Gillmore, JD; Low, SC; Sekijima, Y; Obici, L; Blakesley, R; Arum, S; Shilling, R; Vest, J; Polydefkis, M;
PUBLISHED: 2021, SOURCE: NEUROLOGY, VOLUME: 96, ISSUE: 15
INDEXED IN: WOS
14
TITLE: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTHORS: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 3
INDEXED IN: Scopus WOS
15
TITLE: Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis  Full Text
AUTHORS: Teresa Coelho; Aaron Yarlas; Marcia Waddington Cruz; Michelle K White; Asia Sikora Kessler; Andrew Lovley; Michael Pollock; Spencer Guthrie; Elizabeth J Ackermann; Steven G Hughes; Chafic Karam; Sami Khella; Morie Gertz; Giampaolo Merlini; Laura Obici; Hartmut H Schmidt; Michael Polydefkis; James J B Dyck; Thomas H Brannagan; Isabel Conceicao; Merrill D Benson; John L Berk; ...More
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 4
INDEXED IN: Scopus WOS
16
TITLE: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis (vol 264, pg 703, 2020)  Full Text
AUTHORS: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 3
INDEXED IN: WOS
17
TITLE: Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTHORS: Laura Obici; John L Berk; Alejandra Gonzalez Duarte; Teresa Coelho; Julian Gillmore; Hartmut H J Schmidt; Matthias Schilling; Taro Yamashita; Celine Labeyrie; Thomas H Brannagan; Senda Ajroud Driss; Peter Gorevic; Arnt V Kristen; Jaclyn Franklin; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, VOLUME: 27, ISSUE: 3
INDEXED IN: Scopus WOS
18
TITLE: A phase II, open-label, extension study of long-term patisiran treatment in patients with hereditary transthyretin-mediated (hATTR) amyloidosis  Full Text
AUTHORS: Teresa Coelho; David Adams; Isabel Conceicao; Marcia Waddington Cruz; Hartmut H Schmidt; Juan Buades; Josep Campistol; John L Berk; Michael Polydefkis; Jing Jing Wang; Jihong H Chen; Marianne T Sweetser; Jared Gollob; Ole B Suhr;
PUBLISHED: 2020, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 15, ISSUE: 1
INDEXED IN: Scopus WOS
19
TITLE: Long-Term Efficacy and Safety of Inotersen for Hereditary Transthyretin Amyloidosis: NEURO-TTR Open-Label Extension 2-Year Update
AUTHORS: Thomas Brannagan; Marcia Waddington Cruz; Annabel K Wang; Michael J Polydefkis; Peter J Dyck; Sami Khella; Violaine Plante Bordeneuve; John L Berk; Fabio Barroso; Giampaolo Merlini; Isabel Conceicao; Steven G Hughes; Jesse Kwoh; Shiangtung T W Jung; Spencer Guthrie; Michael Pollock; Merrill D Benson; Morie Gertz; Teresa Coelho;
PUBLISHED: 2019, SOURCE: 71st Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 92, ISSUE: 15
INDEXED IN: WOS
20
TITLE: Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
AUTHORS: Benson, MD; Waddington Cruz, M; Berk, JL; Polydefkis, M; Dyck, PJ; Wang, AK; Plante Bordeneuve, V; Barroso, FA; Merlini, G; Obici, L; Scheinberg, M; Brannagan, TH; Litchy, WJ; Whelan, C; Drachman, BM; Adams, D; Heitner, SB; Conceicao, I; Schmidt, HH; Vita, G; Campistol, JM; Gamez, J; Gorevic, PD; Gane, E; Shah, AM; Solomon, SD; Monia, BP; Hughes, SG; Kwoh, TJ; McEvoy, BW; Jung, SW; Baker, BF; Ackermann, EJ; Gertz, MA; Coelho, T; ...More
PUBLISHED: 2018, SOURCE: NEW ENGLAND JOURNAL OF MEDICINE, VOLUME: 379, ISSUE: 1
INDEXED IN: Scopus WOS
Page 2 of 4. Total results: 37.