31
TITLE: Safety and Efficacy of Inotersen in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (NEURO-TTR)
AUTHORS: Morie Gertz; Annabel K Wang; Teresa Coelho; Marcia Waddington Cruz; Michael J Polydefkis; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Thomas Brannagan; Carol Whelan; Giampaolo Merlini; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Harmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Edward Gane; Peter Gorevic; Acary Souza Bulle Oliveira; Brett P Monia; Steven G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Merrill D Benson; ...More
PUBLISHED: 2018, SOURCE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXED IN: WOS
32
TITLE: Inotersen Improves Norfolk Quality of Life-Diabetic Neuropathy Measures in Patients With Hereditary Transthyretin Amyloidosis with Polyneuropathy in the Phase 3 Study NEURO-TTR
AUTHORS: Michael J Polydefkis; Teresa Coelho; Marcia Waddington Cruz; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Thomas Brannagan; Carol Whelan; Giampaolo Merlini; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Hartmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Edward Gane; Peter Gorevic; Acary Souza B Bulle Oliveira; Brett P Monia; Steven G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Morie Gertz; Merrill D Benson; Annabel K Wang; ...More
PUBLISHED: 2018, SOURCE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXED IN: WOS
33
TITLE: Peptide probes detect misfolded transthyretin oligomers in plasma of hereditary amyloidosis patients
AUTHORS: Joseph D Schonhoft; Cecilia Monteiro; Lars Plate; Yvonne S Eisele; John M Kelly; Daniel Boland; Christopher G Parker; Benjamin F Cravatt; Sergio Teruya; Stephen Helmke; Mathew Maurer; John Berk; Yoshiki Sekijima; Marta Novais; Teresa Coelho; Evan T Powers; Jeffery W Kelly;
PUBLISHED: 2017, SOURCE: SCIENCE TRANSLATIONAL MEDICINE, VOLUME: 9, ISSUE: 407
INDEXED IN: Scopus WOS
34
TITLE: Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study  Full Text
AUTHORS: Ole B Suhr; Teresa Coelho; Juan Buades; Jean Pouget; Isabel Conceicao; John Berk; Hartmut Schmidt; Marcia Waddington Cruz; Josep M Campistol; Brian R Bettencourt; Akshay Vaishnaw; Jared Gollob; David Adams;
PUBLISHED: 2015, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 10, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
35
TITLE: Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis  Full Text
AUTHORS: Morie A Gertz; Merrill D Benson; Peter J Dyck; Martha Grogan; Terresa Coelho; Marcia Cruz; John L Berk; Violaine Plante Bordeneuve; Hartmut H J Schmidt; Giampaolo Merlini;
PUBLISHED: 2015, SOURCE: JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, VOLUME: 66, ISSUE: 21
INDEXED IN: WOS CrossRef
36
TITLE: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTHORS: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLISHED: 2015, SOURCE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, ISSUE: 11
INDEXED IN: WOS CrossRef
37
TITLE: Guideline of transthyretin-related hereditary amyloidosis for clinicians  Full Text
AUTHORS: Yukio Ando; Teresa Coelho; John L Berk; Marcia Waddington Cruz; Bo Goran Ericzon; Shu ichi Ikeda; David D Lewis; Laura Obici; Violaine Plante Bordeneuve; Claudio Rapezzi; Gerard Said; Fabrizio Salvi;
PUBLISHED: 2013, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 8, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
Page 4 of 4. Total results: 37.