Liliana Simões Mendonça
AuthID: R-000-971
11
TITLE: RNA Interference Therapy for Machado-Joseph Disease: Long-Term Safety Profile of Lentiviral Vectors Encoding Short Hairpin RNAs Targeting Mutant Ataxin-3
AUTHORS: Nóbrega, C; Codêsso, JM; Mendonça, L; Pereira De Almeida, L;
PUBLISHED: 2019, SOURCE: Human Gene Therapy, VOLUME: 30, ISSUE: 7
AUTHORS: Nóbrega, C; Codêsso, JM; Mendonça, L; Pereira De Almeida, L;
PUBLISHED: 2019, SOURCE: Human Gene Therapy, VOLUME: 30, ISSUE: 7
INDEXED IN: Scopus
12
TITLE: RNA Interference Therapy for Machado-Joseph Disease: Long-Term Safety Profile of Lentiviral Vectors Encoding Short Hairpin RNAs Targeting Mutant Ataxin-3
AUTHORS: Clevio Nobrega; Jose Miguel Codesso; Liliana Mendonca; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: HUMAN GENE THERAPY, VOLUME: 30, ISSUE: 7
AUTHORS: Clevio Nobrega; Jose Miguel Codesso; Liliana Mendonca; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: HUMAN GENE THERAPY, VOLUME: 30, ISSUE: 7
INDEXED IN: WOS
13
TITLE: Restoring brain cholesterol turnover improves autophagy and has therapeutic potential in mouse models of spinocerebellar ataxia Full Text
AUTHORS: Clevio Nobrega; Liliana Mendonca; Adriana Marcelo; Antonin Lamaziere; Sandra Tome; Gaetan Despres; Carlos A Matos; Fatich Mechmet; Dominique Langui; Wilfred den Dunnen; Luis Pereira de Almeida; Nathalie Cartier; Sandro Alves;
PUBLISHED: 2019, SOURCE: ACTA NEUROPATHOLOGICA, VOLUME: 138, ISSUE: 5
AUTHORS: Clevio Nobrega; Liliana Mendonca; Adriana Marcelo; Antonin Lamaziere; Sandra Tome; Gaetan Despres; Carlos A Matos; Fatich Mechmet; Dominique Langui; Wilfred den Dunnen; Luis Pereira de Almeida; Nathalie Cartier; Sandro Alves;
PUBLISHED: 2019, SOURCE: ACTA NEUROPATHOLOGICA, VOLUME: 138, ISSUE: 5
INDEXED IN: WOS
14
TITLE: Ibuprofen enhances synaptic function and neural progenitors proliferation markers and improves neuropathology and motor coordination in Machado-Joseph disease models
AUTHORS: Liliana S Mendonca; Clevio Nobrega; Silvia Tavino; Maximilian Brinkhaus; Carlos Matos; Sandra Tome; Ricardo Moreira; Daniel Henriques; Brian K Kaspar; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: HUMAN MOLECULAR GENETICS, VOLUME: 28, ISSUE: 22
AUTHORS: Liliana S Mendonca; Clevio Nobrega; Silvia Tavino; Maximilian Brinkhaus; Carlos Matos; Sandra Tome; Ricardo Moreira; Daniel Henriques; Brian K Kaspar; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: HUMAN MOLECULAR GENETICS, VOLUME: 28, ISSUE: 22
INDEXED IN: WOS
15
TITLE: Stem Cell-Based Therapies for Polyglutamine Diseases
AUTHORS: Mendonça, LS; Onofre, I; Miranda, CO; Perfeito, R; Nóbrega, C; de Almeida, LP;
PUBLISHED: 2018, SOURCE: Advances in Experimental Medicine and Biology, VOLUME: 1049
AUTHORS: Mendonça, LS; Onofre, I; Miranda, CO; Perfeito, R; Nóbrega, C; de Almeida, LP;
PUBLISHED: 2018, SOURCE: Advances in Experimental Medicine and Biology, VOLUME: 1049
INDEXED IN: Scopus
16
TITLE: Stem Cell-Based Therapies for Polyglutamine Diseases
AUTHORS: Liliana S Mendonca; Isabel Onofre; Catarina Oliveira Miranda; Rita Perfeito; Clevio Nobrega; Luis Pereira de Almeida;
PUBLISHED: 2018, SOURCE: POLYGLUTAMINE DISORDERS, VOLUME: 1049
AUTHORS: Liliana S Mendonca; Isabel Onofre; Catarina Oliveira Miranda; Rita Perfeito; Clevio Nobrega; Luis Pereira de Almeida;
PUBLISHED: 2018, SOURCE: POLYGLUTAMINE DISORDERS, VOLUME: 1049
INDEXED IN: WOS
17
TITLE: Generation and transplantation of patient-specific iPSC-derived neuroepithelial stem cells for Machado-Joseph disease treatment
AUTHORS: Mendonc, LS; Henriques, D; Moreira, R; Duarte, S; Schwamborn, JC; Pereira de Almeida, LP;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
AUTHORS: Mendonc, LS; Henriques, D; Moreira, R; Duarte, S; Schwamborn, JC; Pereira de Almeida, LP;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
INDEXED IN: WOS
18
TITLE: CYP46A1-gene therapy alleviates spinocerebellar ataxia in mouse models
AUTHORS: Nobrega, C; Mendonca, L; Marcelo, A; Lamaziere, A; Tome, S; Despres, G; Matos, C; Mechmet, F; Langui, D; den Dunnen, W; Pereira de Almeida, LP; Cartier, N; Alves, S;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
AUTHORS: Nobrega, C; Mendonca, L; Marcelo, A; Lamaziere, A; Tome, S; Despres, G; Matos, C; Mechmet, F; Langui, D; den Dunnen, W; Pereira de Almeida, LP; Cartier, N; Alves, S;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
INDEXED IN: WOS
19
TITLE: Safety profile of the intravenous administration of brain-targeted stable nucleic acid lipid particles
AUTHORS: Conceição, M; Mendonça, L; Nóbrega, C; Gomes, C; Costa, P; Hirai, H; Moreira, JN; Lima, MC; Manjunath, N; de Almeida, LP;
PUBLISHED: 2016, SOURCE: Data in Brief, VOLUME: 6
AUTHORS: Conceição, M; Mendonça, L; Nóbrega, C; Gomes, C; Costa, P; Hirai, H; Moreira, JN; Lima, MC; Manjunath, N; de Almeida, LP;
PUBLISHED: 2016, SOURCE: Data in Brief, VOLUME: 6
20
TITLE: Intravenous administration of brain-targeted stable nucleic acid lipid particles alleviates Machado-Joseph disease neurological phenotype Full Text
AUTHORS: Mariana Conceicao; Liliana Mendonca; Clevio Nobrega; Celia Gomes; Pedro Costa; Hirokazu Hirai; Joao Nuno Moreira; Maria C Lima; Manjunath, N; Luis Pereira de Almeida;
PUBLISHED: 2016, SOURCE: BIOMATERIALS, VOLUME: 82
AUTHORS: Mariana Conceicao; Liliana Mendonca; Clevio Nobrega; Celia Gomes; Pedro Costa; Hirokazu Hirai; Joao Nuno Moreira; Maria C Lima; Manjunath, N; Luis Pereira de Almeida;
PUBLISHED: 2016, SOURCE: BIOMATERIALS, VOLUME: 82
INDEXED IN: WOS