23
TITLE: Non-Viral Silencing of Machado-Joseph Disease Through the Systemic Route
AUTHORS: Mariana Conceicao; Liliana Mendonca; Celia Gomes; Pedro Costa; Conceicao Lima; Luis Pereira de Almeida;
PUBLISHED: 2015, SOURCE: 18th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) in MOLECULAR THERAPY, VOLUME: 23
INDEXED IN: WOS
24
TITLE: Re-establishing ataxin-2 downregulates translation of mutant ataxin-3 and alleviates Machado-Joseph disease  Full Text
AUTHORS: Clevio Nobrega; Sara Carmo Silva; David Albuquerque; Ana Vasconcelos Ferreira; Udaya Geetha Vijayakumar; Liliana Mendonca; Hirokazu Hirai; Luis Pereira de Almeida;
PUBLISHED: 2015, SOURCE: BRAIN, VOLUME: 138
INDEXED IN: WOS
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