11
TITLE: Mesenchymal stromal cells to fight SARS-CoV-2: Taking advantage of a pleiotropic therapy
AUTHORS: Barros, I; Silva, A; de Almeida, LP ; Miranda, CO ;
PUBLISHED: 2021, SOURCE: CYTOKINE & GROWTH FACTOR REVIEWS, VOLUME: 58
INDEXED IN: Scopus WOS CrossRef: 19
12
TITLE: Allele-Specific AAV-Based Silencing of Mutant Ataxin-3 Alleviates Neuropathology and Motor Deficits in Spinocerebellar Ataxia Type 3
AUTHORS: Rui Jorge Nobre; Joana Saraiva; Magda Santana; Clelia Fusco; Susana Paixao; Catarina Miranda ; Lorena Petrella; Jose Sereno; Joao Castelhano; Miguel Castelo Branco; Miguel Sena Esteves; Luis Pereira de Almeida;
PUBLISHED: 2020, SOURCE: 23rd Annual Meeting of the American-Society-for-Gene-and-Cell-Therapy in MOLECULAR THERAPY, VOLUME: 28, ISSUE: 4
INDEXED IN: WOS
13
TITLE: Mesenchymal Stromal Cells' Therapy for Polyglutamine Disorders: Where Do We Stand and Where Should We Go?
AUTHORS: Barros, I; Marcelo, A; Silva, TP; Barata, J; Rufino Ramos, D; de Almeida, LP ; Miranda, CO ;
PUBLISHED: 2020, SOURCE: FRONTIERS IN CELLULAR NEUROSCIENCE, VOLUME: 14
INDEXED IN: Scopus WOS CrossRef: 6
14
TITLE: The blood-brain barrier is disrupted in Machado-Joseph disease/spinocerebellar ataxia type 3: evidence from transgenic mice and humanpost-mortemsamples
AUTHORS: Lobo, DD; Nobre, RJ ; Miranda, CO ; Pereira, D; Castelhano, J; Sereno, J; Koeppen, A; Castelo Branco, M; de Almeida, LP ;
PUBLISHED: 2020, SOURCE: ACTA NEUROPATHOLOGICA COMMUNICATIONS, VOLUME: 8, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef: 17
15
TITLE: A miRNA-based gene therapy approach to knock-down mutant ATXN3: Alleviation of Machado-Joseph disease phenotype in two mouse models upon two routes of administration  Full Text
AUTHORS: Rui Jorge Nobre; Joana Saraiva; Clelia Fusco; Susana Paixao; Magda Santana; Catarina Miranda ; Lorena Petrella; Jose Sereno; Joao Castelhano; Miguel Castelo Branco; Miguel Sena Esteves; Luis Almeida;
PUBLISHED: 2019, SOURCE: EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 49
INDEXED IN: WOS
16
TITLE: Autophagy activation induced by let-7 microRNA overexpression counteracts disease phenotype in Machado-Joseph disease mouse models
AUTHORS: Sónia Duarte; Beatriz Estremores; Janete Cunha-Santos; Catarina Miranda ; João Barata; Albert La Spada; Luis De Almeida;
PUBLISHED: 2019, SOURCE: Frontiers in Cellular Neuroscience, VOLUME: 13
INDEXED IN: CrossRef
17
TITLE: Blood-brain barrier dysfunction as a neuropathological feature in Machado-Joseph Disease: results from human and mouse samples
AUTHORS: Diana Lobo; Rui Nobre ; Catarina Miranda ; Dina Pereira; João Castelhano; José Sereno; Miguel Castelo-Branco; Luís De Almeida ;
PUBLISHED: 2019, SOURCE: Frontiers in Cellular Neuroscience, VOLUME: 13
INDEXED IN: CrossRef
18
TITLE: CRISPR interference-mediated silencing of mutant ATXN3 decreases motor impairments of an in vivo Machado-Joseph disease model  Full Text
AUTHORS: Carlos Matos; Frederico Pena; Andre Conceicao; Sara Lopes; Sonia Duarte; Catarina Miranda ; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 49
INDEXED IN: WOS
19
TITLE: CRISPR-Cas9-Mediated Pre-Transcriptional Silencing of Mutant ATXN3 Decreases Motor Impairments of an In Vivo Machado-Joseph Disease Model
AUTHORS: Carlos Matos; Frederico Pena; Andre Conceicao; Sara Lopes; Sonia Duarte; Catarina Miranda ; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: 22nd Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) in MOLECULAR THERAPY, VOLUME: 27, ISSUE: 4
INDEXED IN: WOS
20
TITLE: Non-invasive and allele-specific silencing therapy for Polyglutamine disorders: the case of Machado-Joseph disease/Spinocerebellar ataxia type 3
AUTHORS: Rui Nobre ; Joana Saraiva; Susana Paixão; Cellia Fusco; Magda Santana; Catarina Miranda ; Lorena Petrella; Jose Sereno; Joao Castelhano; Miguel Castelo-Branco; Miguel Sena-Esteves; Luis Pereira De ALmeida ;
PUBLISHED: 2019, SOURCE: Frontiers in Cellular Neuroscience, VOLUME: 13
INDEXED IN: CrossRef
Page 2 of 4. Total results: 33.