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TITLE: Extracellular vesicles-associated AAVs for the treatment of Machado-Joseph disease
AUTHORS: Henriques, Carina; Albuquerque, Patricia; Rufino Ramos, David; Lopes, Miguel M.; Leandro, Kevin; Miranda, Catarina O. ; Almeida, Rita; Lopes Gabriel, Guilherme; de Sousa Lourenco, Joao; Lopes, Sara M.; Gaspar, Laetitia S.; Lobo, Diana D.; Silva, Ana Carolina; Ribeiro Rodrigues, Teresa M.; Girao, Henrique; Gomes, Celia M.; Baganha, Rafael; Duarte, Sonia ; Maguire, Casey A.; Santana, Magda M.; de Almeida, Luis Pereira ; Nobre, Rui Jorge; ...More
PUBLISHED: 2026, SOURCE: MOLECULAR THERAPY, VOLUME: 34, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
2
TITLE: rAAV-Delivered Bicistronic Artificial microRNAs for Allele-Specific Silencing Improve Motor and Molecular Outcomes in Spinocerebellar Ataxia Type 3
AUTHORS: Ana Carolina Silva; Carina Henriques; Diana D Lobo; Ana Rita Fernandes; Miguel M Lopes; Kevin Leandro; Dina Pereira; Sónia P Duarte ; Sara M Lopes; Magda M Santana; Amal Dakka; Steve De Marco; Marla Weetall; Jana Narasimhan; Anu Bhattacharyya; Rui Jorge Nobre; Luís Pereira de Almeida ;
PUBLISHED: 2025
INDEXED IN: CrossRef
3
TITLE: A gut miRNA targets cardiolipin synthase and affects mitochondrial function: relevance for Parkinson's disease  Full Text
AUTHORS: Guedes, Beatriz; Duarte, Sonia ; Cardoso, Sandra Morais; Esteves, Ana Raquel;
PUBLISHED: 2024, SOURCE: Mitochondria in Aging, Cancer and Cell Death Conference in BIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR BASIS OF DISEASE, VOLUME: 1870, ISSUE: 8
INDEXED IN: WOS CrossRef
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TITLE: Graft-derived neurons and bystander effects are maintained for six months after human iPSC-derived NESC transplantation in mice's cerebella
AUTHORS: Liliana Mendonça; Daniel Henriques; Vanessa Fernandes; Ricardo Moreira; João Brás; Sónia Duarte ; Jens Schwamborn; Luís Pereira de Almeida ;
PUBLISHED: 2024, SOURCE: Scientific reports, VOLUME: 14, ISSUE: 1
INDEXED IN: Scopus CrossRef
5
TITLE: MiRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3
AUTHORS: Nobre, RJ ; Lobo, DD; Henriques, C; Duarte, SP ; Lopes, SM; Silva, AC; Lopes, MM; Mariet, F; Schwarz, LK; Baatje, MS; Ferreira, V; Valles, A; de Almeida, LP ; Evers, MM; Toonen, LJA;
PUBLISHED: 2022, SOURCE: NUCLEIC ACID THERAPEUTICS, VOLUME: 32, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef: 10
6
TITLE: Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disorders
AUTHORS: Silva, AC; Lobo, DD; Martins, IM; Lopes, SM; Henriques, C; Duarte, SP ; Dodart, JC; Nobre, RJ ; de Almeida, LP ;
PUBLISHED: 2020, SOURCE: BRAIN, VOLUME: 143, ISSUE: 2
INDEXED IN: Scopus WOS CrossRef: 56
7
TITLE: Autophagy activation induced by let-7 microRNA overexpression counteracts disease phenotype in Machado-Joseph disease mouse models
AUTHORS: Sónia Duarte ; Beatriz Estremores; Janete Cunha-Santos; Catarina Miranda ; João Barata; Albert La Spada; Luis De Almeida;
PUBLISHED: 2019, SOURCE: Frontiers in Cellular Neuroscience, VOLUME: 13
INDEXED IN: CrossRef
8
TITLE: Molecular Mechanisms and Cellular Pathways Implicated in Machado-Joseph Disease Pathogenesis
AUTHORS: Nóbrega, C ; Simões, AT; Duarte Neves, J; Duarte, S ; Vasconcelos Ferreira, A; Cunha Santos, J; Pereira, D; Santana, M; Cavadas, C ; de Almeida, LP ;
PUBLISHED: 2018, SOURCE: Advances in Experimental Medicine and Biology, VOLUME: 1049
INDEXED IN: Scopus CrossRef: 19
9
TITLE: Repeated Mesenchymal Stromal Cell Treatment Sustainably Alleviates Machado-Joseph Disease
AUTHORS: Miranda, CO ; Marcelo, A; Silva, TP; Barata, J; Vasconcelos Ferreira, A; Pereira, D; Nobrega, C ; Duarte, S ; Barros, I; Alves, J; Sereno, J; Petrella, LI; Castelhano, J; Paiva, VH; Paulo Rodrigues-Santos ; Alves, V; Nunes Correia, I; Nobre, RJ ; Gomes, C; Castelo Branco, M; de Almeida, LP ; ...More
PUBLISHED: 2018, SOURCE: MOLECULAR THERAPY, VOLUME: 26, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef: 23
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TITLE: Let-7 Coordinately Suppresses Components of the Amino Acid Sensing Pathway to Repress mTORC1 and Induce Autophagy
AUTHORS: Amy N Dubinsky; Somasish Ghosh Dastidar; Cynthia L Hsu; Rabaab Zahra; Stevan N Djakovic; Sonia Duarte ; Christine C Esau; Brian Spencer; Travis D Ashe; Kimberlee M Fischer; Deidre A MacKenna; Bryce L Sopher; Eliezer Masliah; Terry Gaasterland; Nelson N Chau; Luis Pereira de Almeida; Bradley E Morrison; Albert R La Spada;
PUBLISHED: 2014, SOURCE: CELL METABOLISM, VOLUME: 20, ISSUE: 4
INDEXED IN: Scopus WOS CrossRef
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