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TITLE: Repeated transplantation of mesenchymal stromal cells in Machado-Joseph disease/Spinocerebellar ataxia type-3 mice can sustainably alleviate phenotypic symptoms and ameliorations can be monitored through magnetic resonance spectroscopy  Full Text
AUTHORS: Catarina Oliveira Miranda ; Adriana Marcelo; Teresa Pereira Silva; Joao Barata; Ana Vasconcelos Ferreira; Dina Pereira; Sonia Duarte; Ines Barros; Clevio Nobrega; Jose Sereno; Lorena Petrella; Vitor Hugo Paiva; Joao Castelhano; Rui Jorge Nobre; Celia Gomes; Miguel Castelo Branco; Luis Pereira de Almeida;
PUBLISHED: 2019, SOURCE: EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 49
INDEXED IN: WOS
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TITLE: Assessing cerebellar neurometabolic biomarkers by in vivo magnetic resonance spectroscopy in a transgenic mouse model of Machado-Joseph disease
AUTHORS: Miranda, CO ; Nobre, RJ; Paiva, VH; Castelhano, J; Petrella, L; Sereno, J; Castelo Branco, M; Pereira de Almeida, LP;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
INDEXED IN: WOS
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TITLE: Let-7 microRNA overexpression mediated by lentivirus alleviates neuropathology, balance and motor deficits in Machado-Joseph disease mouse models
AUTHORS: Duarte, SP; Estremores, B; Cunha Santos, J; Miranda, CO ; Barata, J; La Spada, AR; de Almeida, LP;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
INDEXED IN: WOS
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TITLE: Repeated Mesenchymal Stromal Cell Treatment Sustainably Alleviates Machado-Joseph Disease
AUTHORS: Miranda, CO ; Marcelo, A; Silva, TP; Barata, J; Vasconcelos Ferreira, A; Pereira, D; Nobrega, C ; Duarte, S ; Barros, I; Alves, J; Sereno, J; Petrella, LI; Castelhano, J; Paiva, VH; Paulo Rodrigues-Santos ; Alves, V; Nunes Correia, I; Nobre, RJ ; Gomes, C; Castelo Branco, M; de Almeida, LP ; ...More
PUBLISHED: 2018, SOURCE: MOLECULAR THERAPY, VOLUME: 26, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef: 23
26
TITLE: Repeated mesenchymal stromal cells treatment sustainably alleviates Machado-Joseph disease/spinocerebellar ataxia type-3
AUTHORS: Miranda, CO ; Marcelo, A; Silva, TP; Barata, J; Vasconcelos Ferreira, A; Pereira, D; Duarte, S; Nobrega, C; Sereno, J; Petrella, L; Paiva, VH; Castelhano, J; Nobre, RJ; Gomes, C; Castelo Branco, M; Pereira de Almeida, LP;
PUBLISHED: 2018, SOURCE: Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy in HUMAN GENE THERAPY, VOLUME: 29, ISSUE: 12
INDEXED IN: WOS
27
TITLE: Stem Cell-Based Therapies for Polyglutamine Diseases
AUTHORS: Mendonça, LS; Onofre, I; Miranda, CO ; Perfeito, R ; Nóbrega, C ; de Almeida, LP ;
PUBLISHED: 2018, SOURCE: Advances in Experimental Medicine and Biology, VOLUME: 1049
INDEXED IN: Scopus CrossRef: 13
28
TITLE: Stem Cell-Based Therapies for Polyglutamine Diseases
AUTHORS: Mendonca, LS; Onofre, I; Miranda, CO ; Perfeito, R; Nobrega, C; de Almeida, LP;
PUBLISHED: 2018, SOURCE: POLYGLUTAMINE DISORDERS, VOLUME: 1049
INDEXED IN: WOS
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