1
TITLE: Graft-derived neurons and bystander effects are maintained for six months after human iPSC-derived NESC transplantation in mice's cerebella
AUTHORS: Liliana Mendonça; Daniel Henriques; Vanessa Fernandes; Ricardo Moreira; João Brás; Sónia Duarte ; Jens Schwamborn; Luís Pereira de Almeida ;
PUBLISHED: 2024, SOURCE: Scientific reports, VOLUME: 14, ISSUE: 1
INDEXED IN: Scopus CrossRef
2
TITLE: MiRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3
AUTHORS: Nobre, RJ ; Lobo, DD; Henriques, C; Duarte, SP ; Lopes, SM; Silva, AC; Lopes, MM; Mariet, F; Schwarz, LK; Baatje, MS; Ferreira, V; Valles, A; de Almeida, LP ; Evers, MM; Toonen, LJA;
PUBLISHED: 2022, SOURCE: NUCLEIC ACID THERAPEUTICS, VOLUME: 32, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef: 10
3
TITLE: Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disorders
AUTHORS: Silva, AC; Lobo, DD; Martins, IM; Lopes, SM; Henriques, C; Duarte, SP ; Dodart, JC; Nobre, RJ ; de Almeida, LP ;
PUBLISHED: 2020, SOURCE: BRAIN, VOLUME: 143, ISSUE: 2
INDEXED IN: Scopus WOS CrossRef: 56
4
TITLE: Molecular Mechanisms and Cellular Pathways Implicated in Machado-Joseph Disease Pathogenesis
AUTHORS: Nóbrega, C ; Simões, AT; Duarte Neves, J; Duarte, S ; Vasconcelos Ferreira, A; Cunha Santos, J; Pereira, D; Santana, M; Cavadas, C ; de Almeida, LP ;
PUBLISHED: 2018, SOURCE: Advances in Experimental Medicine and Biology, VOLUME: 1049
INDEXED IN: Scopus CrossRef: 19
5
TITLE: Repeated Mesenchymal Stromal Cell Treatment Sustainably Alleviates Machado-Joseph Disease
AUTHORS: Miranda, CO ; Marcelo, A; Silva, TP; Barata, J; Vasconcelos Ferreira, A; Pereira, D; Nobrega, C ; Duarte, S ; Barros, I; Alves, J; Sereno, J; Petrella, LI; Castelhano, J; Paiva, VH; Paulo Rodrigues-Santos ; Alves, V; Nunes Correia, I; Nobre, RJ ; Gomes, C; Castelo Branco, M; de Almeida, LP ; ...More
PUBLISHED: 2018, SOURCE: MOLECULAR THERAPY, VOLUME: 26, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef: 23
6
TITLE: Let-7 Coordinately Suppresses Components of the Amino Acid Sensing Pathway to Repress mTORC1 and Induce Autophagy
AUTHORS: Amy N Dubinsky; Somasish Ghosh Dastidar; Cynthia L Hsu; Rabaab Zahra; Stevan N Djakovic; Sonia Duarte ; Christine C Esau; Brian Spencer; Travis D Ashe; Kimberlee M Fischer; Deidre A MacKenna; Bryce L Sopher; Eliezer Masliah; Terry Gaasterland; Nelson N Chau; Luis Pereira de Almeida; Bradley E Morrison; Albert R La Spada;
PUBLISHED: 2014, SOURCE: CELL METABOLISM, VOLUME: 20, ISSUE: 4
INDEXED IN: Scopus WOS CrossRef
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TITLE: Cationic Liposome-Based Systems for Nucleic Acid Delivery: From the Formulation Development to Therapeutic Applications
AUTHORS: Henrique Faneca; Ana Luísa Cardoso ; Sara Trabulo; Sónia Duarte ; Maria Pedroso P de Lima;
PUBLISHED: 2013, SOURCE: Drug Delivery Systems: Advanced Technologies Potentially Applicable in Personalised Treatment - Advances in Predictive, Preventive and Personalised Medicine
INDEXED IN: CrossRef
8
TITLE: Gene silencing as a promising strategy to target CNS and neurological disorders
AUTHORS: Cardoso, AL ; Trabulo, SM; Duarte, SP ; Costa, PM; Almeida, LP ; de Lima, MCP;
PUBLISHED: 2013, SOURCE: Gene Silencing: Theory, Techniques and Applications
INDEXED IN: Scopus
9
TITLE: Preventive Cancer Stem Cell-Based Vaccination Reduces Liver Metastasis Development in a Rat Colon Carcinoma Syngeneic Model  Full Text
AUTHORS: Sonia Duarte ; David Momier; Patrick Baque; Vincent Casanova; Agnes Loubat; Michel Samson; Jean Marie Guigonis; Pascal Staccini; Marie Christine Saint Paul; Maria Pedroso De Lima ; Georges F Carle; Valerie Pierrefite Carle ;
PUBLISHED: 2013, SOURCE: STEM CELLS, VOLUME: 31, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef
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