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TITLE: Plasmid Gene Therapy for Monogenic Disorders: Challenges and Perspectives  Full Text
AUTHORS: Luis, Marco A.; Goes, Marcelo A. D.; Santos, Fatima Milhano; Mesquita, Joana; Tavares Ratado, Paulo; Tomaz, Candida Teixeira;
PUBLISHED: 2025, SOURCE: PHARMACEUTICS, VOLUME: 17, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef