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TITLE: Gene Therapies for Polyglutamine Diseases
AUTHORS: Carlos A Matos; Vitor Carmona; Udaya Geetha Vijayakumar; Sara Lopes; Patricia Albuquerque; Mariana Conceicao; Rui Jorge Nobre; Clevio Nobrega; Luis Pereira de Almeida;
PUBLISHED: 2018, SOURCE: POLYGLUTAMINE DISORDERS, VOLUME: 1049
INDEXED IN: Scopus WOS
2
TITLE: Unravelling Endogenous MicroRNA System Dysfunction as a New Pathophysiological Mechanism in Machado-Joseph Disease
AUTHORS: Vitor Carmona; Janete Cunha Santos; Isabel Onofre; Ana Teresa Simoes; Udaya Vijayakumar; Beverly L Davidson; Luis Pereira de Almeida;
PUBLISHED: 2017, SOURCE: MOLECULAR THERAPY, VOLUME: 25, ISSUE: 4
INDEXED IN: Scopus WOS
3
TITLE: Role of MicroRNA Deregulation in Machado-Joseph Disease
AUTHORS: Udaya Geetha Vijayakumar; Vitor Carmona; Clevio Nobrega; Ligia Ferreira; Luis Pereira de Almeida;
PUBLISHED: 2015, SOURCE: 18th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) in MOLECULAR THERAPY, VOLUME: 23
INDEXED IN: WOS
4
TITLE: Re-establishing ataxin-2 downregulates translation of mutant ataxin-3 and alleviates Machado-Joseph disease  Full Text
AUTHORS: Clevio Nobrega; Sara Carmo Silva; David Albuquerque; Ana Vasconcelos Ferreira; Udaya Geetha Vijayakumar; Liliana Mendonca; Hirokazu Hirai; Luis Pereira de Almeida;
PUBLISHED: 2015, SOURCE: BRAIN, VOLUME: 138
INDEXED IN: WOS