1
TITLE: Characteristics of Patients with Hereditary Transthyretin Amyloidosis-Polyneuropathy (ATTRv-PN) in NEURO-TTRansform, an Open-label Phase 3 Study of Eplontersen
AUTHORS: Coelho, Teresa; Cruz, Marcia Waddington; Chao, Chi Chao; Parman, Yesim; Wixner, Jonas; Weiler, Markus; Barroso, Fabio A.; Dasgupta, Noel R.; Jung, Shiangtung W.; Schneider, Eugene; Viney, Nicholas J.; Dyck, P. James B.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Gertz, Morie A.; Obici, Laura; Berk, John L.;
PUBLISHED: 2022, SOURCE: NEUROLOGY AND THERAPY
INDEXED IN: Scopus WOS
2
TITLE: Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-L-Rx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
AUTHORS: Coelho, T; Ando, Y; Benson, MD; Berk, JL; Waddington Cruz, M; Dyck, PJ; Gillmore, JD; Khella, SL; Litchy, WJ; Obici, L; Monteiro, C; Tai, LJ; Viney, NJ; Buchele, G; Brambatti, M; Jung, SW; O'Dea, LS; Tsimikas, S; Schneider, E; Geary, RS; Monia, BP; Gertz, M; ...More
PUBLISHED: 2021, SOURCE: NEUROLOGY AND THERAPY
INDEXED IN: Scopus WOS
3
TITLE: ATTR amyloidosis during the COVID-19 pandemic: insights from a global medical roundtable  Full Text
AUTHORS: Brannagan, TH; Auer Grumbach, M; Berk, JL; Briani, C; Bril, V; Coelho, T; Damy, T; Dispenzieri, A; Drachman, BM; Fine, N; Gaggin, HK; Gertz, M; Gillmore, JD; Gonzalez, E; Hanna, M; Hurwitz, DR; Khella, SL; Maurer, MS; Nativi Nicolau, J; Olugemo, K; Quintana, LF; Rosen, AM; Schmidt, HH; Shehata, J; Waddington Cruz, M; Whelan, C; Ruberg, FL; ...More
PUBLISHED: 2021, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 16, ISSUE: 1
INDEXED IN: Scopus WOS
4
TITLE: Long-term Outcomes of Sequential Hematopoietic Stem Cell Transplantation and Kidney Transplantation: Single-center Experience
AUTHORS: Moreira, Carla Leal; Hasib Sidiqi, M.; Buadi, Francis K.; Litzow, Mark R.; Gertz, Morie A.; Dispenzieri, Angela; Russell, Stephen J.; Ansell, Stephen M.; Stegall, Mark D.; Prieto, Mikel; Dean, Patrick G.; Nyberg, Scott L.; El Ters, Mireille; Hogan, William J.; Amer, Hatem; Cosio, Fernando G.; Leung, Nelson;
PUBLISHED: 2021, SOURCE: TRANSPLANTATION, VOLUME: 105, ISSUE: 7
INDEXED IN: Scopus WOS
5
TITLE: Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis  Full Text
AUTHORS: Teresa Coelho; Aaron Yarlas; Marcia Waddington Cruz; Michelle K White; Asia Sikora Kessler; Andrew Lovley; Michael Pollock; Spencer Guthrie; Elizabeth J Ackermann; Steven G Hughes; Chafic Karam; Sami Khella; Morie Gertz; Giampaolo Merlini; Laura Obici; Hartmut H Schmidt; Michael Polydefkis; James J B Dyck; Thomas H Brannagan; Isabel Conceicao; Merrill D Benson; John L Berk; ...More
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 4
INDEXED IN: Scopus WOS
6
TITLE: Expert consensus recommendations to improve diagnosis of ATTR amyloidosis with polyneuropathy  Full Text
AUTHORS: David Adams; Yukio Ando; Joao Melo Beirao; Teresa Coelho; Morie A Gertz; Julian D Gillmore; Philip N Hawkins; Isabelle Lousada; Ole B Suhr; Giampaolo Merlini;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY
INDEXED IN: Scopus WOS
7
TITLE: Management of Thrombocytopenia in Patients With Hereditary Transthyretin Amyloidosis Treated With Inotersen: Clinical Trial and Postmarketing Surveillance Experience  Full Text
AUTHORS: Gertz, M; Khella, S; Wang, A; Coelho, T; Waddington Cruz, MW; Polydefkis, MJ; Plante Bordeneuve, V; Berk, JL; Barroso, F; Brannagan H B Iii; Merlini, G; Obici, L; Conceicao, I; Jung, SW; Hughes, SG; Aquino, P; O'dea, LSL; Narayana, A; Dasgupta, N; Benson, MD;
PUBLISHED: 2020, SOURCE: 6th Congress of the European-Academy-of-Neurology (EAN) in EUROPEAN JOURNAL OF NEUROLOGY, VOLUME: 27
INDEXED IN: WOS
8
TITLE: Rationale and Design of NEURO-TTRansform, a Phase 3 Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx (ION-682884) in Patients with Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
AUTHORS: Sami Khella; Morie A Gertz; Teresa Coelho; Cecilia Monteiro; Li Jung Tai; Nicholas Viney; Gustavo Buchele; Michela Brambatti; Sotirios Tsimikas; Shiangtung T Jung; Louis St. L O'Dea; Eugene Schneider; Richard Geary; Brett Monia;
PUBLISHED: 2020, SOURCE: Annual Meeting of the American-Academy-of-Neurology in NEUROLOGY, VOLUME: 94, ISSUE: 15
INDEXED IN: WOS
9
TITLE: Avoiding misdiagnosis: expert consensus recommendations for the suspicion and diagnosis of transthyretin amyloidosis for the general practitioner  Full Text
AUTHORS: Morie Gertz; David Adams; Yukio Ando; Joao Melo Beirao; Sabahat Bokhari; Teresa Coelho; Raymond L Comenzo; Thibaud Damy; Sharmila Dorbala; Brian M Drachman; Marianna Fontana; Julian D Gillmore; Martha Grogan; Philip N Hawkins; Isabelle Lousada; Arnt V Kristen; Frederick L Ruberg; Ole B Suhr; Mathew S Maurer; Jose Nativi Nicolau; Candida Cristina Quarta; Claudio Rapezzi; Ronald Witteles; Giampaolo Merlini; ...More
PUBLISHED: 2020, SOURCE: BMC FAMILY PRACTICE, VOLUME: 21, ISSUE: 1
INDEXED IN: Scopus WOS
10
TITLE: Advances in the treatment of hereditary transthyretin amyloidosis: A review  Full Text
AUTHORS: Morie A Gertz; Michelle L Mauermann; Martha Grogan; Teresa Coelho;
PUBLISHED: 2019, SOURCE: BRAIN AND BEHAVIOR, VOLUME: 9, ISSUE: 9
INDEXED IN: Scopus WOS
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