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TITLE: Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative
AUTHORS: Derralynn A Hughes; Patricio Aguiar; Patrick B Deegan; Fatih Ezgu; Andrea Frustaci; Olivier Lidove; Ales Linhart; Jean Claude Lubanda; James C Moon; Kathleen Nicholls; Dau Ming Niu; Albina Nowak; Uma Ramaswami; Ricardo Reisin; Paula Rozenfeld; Raphael Schiffmann; Einar Svarstad; Mark Thomas; Roser Torra; Bojan Vujkovac; David G Warnock; Michael L West; Jack Johnson; Mark J Rolfe; Sandro Feriozzi; ...More
PUBLISHED: 2020, SOURCE: BMJ OPEN, VOLUME: 10, ISSUE: 10
INDEXED IN: Scopus WOS
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TITLE: Dialysis and Transplantation in Fabry Disease: Indications for Enzyme Replacement Therapy
AUTHORS: Renzo Mignani; Sandro Feriozzi; Roland M Schaefer; Frank Breunig; Oliveira, JP ; Piero Ruggenenti; Gere Sunder Plassmann;
PUBLISHED: 2010, SOURCE: CLINICAL JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY, VOLUME: 5, ISSUE: 2
INDEXED IN: Scopus WOS CrossRef: 24