1
TITLE: Additive Potentiation of R334W-CFTR Function by Novel Small Molecules
AUTHORS: Bacalhau, Mafalda; Ferreira, Filipa C.; Silva, Iris A. L.; Buarque, Camilla D.; Amaral, Margarida D.; Lopes Pacheco, Miqueias;
PUBLISHED: 2023, SOURCE: JOURNAL OF PERSONALIZED MEDICINE, VOLUME: 13, ISSUE: 1
INDEXED IN: Scopus WOS
2
TITLE: Rescue of Mutant CFTR Trafficking Defect by the Investigational Compound MCG1516A  Full Text
AUTHORS: Lopes Pacheco, M; Bacalhau, M; Ramalho, SS; Silva, IAL; Ferreira, FC; Carlile, GW; Thomas, DY; Farinha, CM; Hanrahan, JW; Amaral, MD;
PUBLISHED: 2022, SOURCE: CELLS, VOLUME: 11, ISSUE: 1
INDEXED IN: Scopus WOS
3
TITLE: Systems Approaches to Unravel Molecular Function: High-content siRNA Screen Identifies TMEM16A Traffic Regulators as Potential Drug Targets for Cystic Fibrosis  Full Text
AUTHORS: Pinto, Madalena C.; Botelho, Hugo M.; Silva, Iris A. L.; Railean, Violeta; Neumann, Beate; Pepperkok, Rainer; Schreiber, Rainer; Kunzelmann, Karl; Amaral, Margarida D.;
PUBLISHED: 2022, SOURCE: JOURNAL OF MOLECULAR BIOLOGY, VOLUME: 434, ISSUE: 5
INDEXED IN: Scopus WOS
4
TITLE: Rare Trafficking CFTR Mutations Involve Distinct Cellular Retention Machineries and Require Different Rescuing Strategies  Full Text
AUTHORS: Ramalho, SS; Silva, IAL; Amaral, MD; Farinha, CM;
PUBLISHED: 2022, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 23, ISSUE: 1
INDEXED IN: WOS
6
TITLE: New drugs in cystic fibrosis: what has changed in the last decade?
AUTHORS: Roda, Juliana; Pinto Silva, Catarina; Silva, Iris A. I.; Maia, Carla; Almeida, Susana; Ferreira, Ricardo; Oliveira, Guiomar;
PUBLISHED: 2022, SOURCE: THERAPEUTIC ADVANCES IN CHRONIC DISEASE, VOLUME: 13
INDEXED IN: WOS
7
TITLE: Absence of EPAC1 Signaling to Stabilize CFTR in Intestinal Organoids  Full Text
AUTHORS: Ferreira, Joao F.; Silva, Iris A. L.; Botelho, Hugo M.; Amaral, Margarida D.; Farinha, Carlos M.;
PUBLISHED: 2022, SOURCE: CELLS, VOLUME: 11, ISSUE: 15
INDEXED IN: Scopus WOS
8
TITLE: Editorial: Mechanisms of Novel Drugs and Gene Modifiers in the Treatment of Cystic Fibrosis
AUTHORS: Veit, Guido; Silva, Iris; Conese, Massimo; Laselva, Onofrio;
PUBLISHED: 2022, SOURCE: FRONTIERS IN MOLECULAR BIOSCIENCES, VOLUME: 9
INDEXED IN: Scopus WOS
9
TITLE: Measuring cystic fibrosis drug responses in organoids derived from 2D differentiated nasal epithelia
AUTHORS: Amatngalim, Gimano D.; Rodenburg, Lisa W.; Aalbers, Bente L.; Raeven, Henriette H. M.; Aarts, Ellen M.; Sarhane, Dounia; Spelier, Sacha; Lefferts, Juliet W.; Silva, Iris A. L.; Nijenhuis, Wilco; Vrendenbarg, Sacha; Kruisselbrink, Evelien; Brunsveld, Jesse E.; van Drunen, Cornelis M.; Michel, Sabine; de Winter de Groot, Karin M.; Heijerman, Harry G.; Kapitein, Lukas C.; Amaral, Magarida D.; van der Ent, Cornelis K.; Beekman, Jeffrey M.; ...More
PUBLISHED: 2022, SOURCE: LIFE SCIENCE ALLIANCE, VOLUME: 5, ISSUE: 12
INDEXED IN: Scopus WOS
10
TITLE: Advances in Preclinical In Vitro Models for the Translation of Precision Medicine for Cystic Fibrosis
AUTHORS: Silva, Iris A. L.; Laselva, Onofrio; Lopes Pacheco, Miqueias;
PUBLISHED: 2022, SOURCE: JOURNAL OF PERSONALIZED MEDICINE, VOLUME: 12, ISSUE: 8
INDEXED IN: Scopus WOS
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