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TITLE: Retinal Organoids from an AIPL1 CRISPR/Cas9 Knockout Cell Line Successfully Recapitulate the Molecular Features of LCA4 Disease  Full Text
AUTHORS: Perdigao, Pedro R. L.; Ollington, Bethany; Sai, Hali; Leung, Amy; Sacristan Reviriego, Almudena; van der Spuy, Jacqueline;
PUBLISHED: 2023, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 24, ISSUE: 6
INDEXED IN: WOS
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TITLE: Extracellular communication between brain cells through functional transfer of Cre mRNA mediated by extracellular vesicles
AUTHORS: Rufino Ramos, David; Leandro, Kevin; Perdigao, Pedro R. L.; O'Brien, Killian; Pinto, Maria Manuel; Santana, Magda M.; van Solinge, Thomas S.; Mahjoum, Shadi; Breakefield, Xandra O.; Breyne, Koen; de Almeida, Luis Pereira;
PUBLISHED: 2023, SOURCE: MOLECULAR THERAPY, VOLUME: 31, ISSUE: 7
INDEXED IN: Scopus WOS
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TITLE: Protein Delivery of Cell-Penetrating Zinc-Finger Activators Stimulates Latent HIV-1-Infected Cells
AUTHORS: Pedro R L Perdigao; Catarina Cunha Santos; Carlos F Barbas; Mariana Santa Marta; Joao Goncalves;
PUBLISHED: 2020, SOURCE: MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, VOLUME: 18
INDEXED IN: WOS