1
TITLE: Sickle cell disease landscape and challenges in the EU the ERN-EuroBloodNet perspective
AUTHORS: Pereira, Maria del Mar Manu; Colombatti, Raffaella; Alvarez, Federico; Bartolucci, Pablo; Bento, Celeste; Brunetta, Angelo Loris; Cela, Elena; Christou, Soteroula; Collado, Anna; de Montalembert, Mariane; Dedeken, Laurence; Fenaux, Pierre; Galacteros, Frederic; Glenthoj, Andreas; Valle, Victoria Gutierrez; Kattamis, Antonis; Kunz, Joachim; Lobitz, Stephan; McMahon, Corrina; Pellegrini, Mariangela; Reidel, Sara; Russo, Giovanna; Freire, Miriam Santos; van Beers, Eduard; Kountouris, Petros; Gulbis, Beatrice; ...More
PUBLISHED: 2023, SOURCE: LANCET HAEMATOLOGY, VOLUME: 10, ISSUE: 8
INDEXED IN: Scopus WOS
2
TITLE: Ruxolitinib is more effective than other JAK inhibitors to treat VEXAS syndrome: a retrospective multicenter study
AUTHORS: Heiblig, Mael; Ferrada, Marcela A.; Koster, Matthew T.; Barba, Thomas; Gerfaud Valentin, Mathieu; Mekinian, Arsene; Coelho, Henrique; Fossard, Gaelle; Barraco, Fiorenza; Galicier, Lionel; Bienvenu, Boris; Hirsch, Pierre; Vial, Guillaume; Boutin, Anne Blandine; Galland, Joris; Le Guenno, Guillaume; Bigot, Adrien; Warrington, Kenneth J.; Kermani, Tanaz A.; Grayson, Peter C.; Patel, Bhavisha A.; Beck, David B.; Jamilloux, Yvan; Fenaux, Pierre; Sujobert, Pierre; ...More
PUBLISHED: 2022, SOURCE: BLOOD, VOLUME: 140, ISSUE: 8
INDEXED IN: WOS
3
TITLE: Phase III, Randomized, Placebo-Controlled Trial of CC-486 (Oral Azacitidine) in Patients With Lower-Risk Myelodysplastic Syndromes
AUTHORS: Garcia Manero, G; Santini, V; Almeida, A; Platzbecker, U; Jonasova, A; Silverman, LR; Falantes, J; Reda, G; Buccisano, F; Fenaux, P; Buckstein, R; Campelo, MD; Larsen, S; Valcarcel, D; Vyas, P; Giai, V; Oliva, EN; Shortt, J; Niederwieser, D; Mittelman, M; Fianchi, L; La Torre, I; Zhong, JH; Laille, E; de Menezes, DL; Skikne, B; Beach, CL; Giagounidis, A; ...More
PUBLISHED: 2021, SOURCE: JOURNAL OF CLINICAL ONCOLOGY, VOLUME: 39, ISSUE: 13
INDEXED IN: Scopus WOS
4
TITLE: Clinical Efficacy of JAK Inhibitors in Patients with Vexas Syndrome: A Multicenter Retrospective Study
AUTHORS: Heiblig, Mael; Ferrada, Marcela A.; Gerfaud Valentin, Mathieu; Barba, Thomas; Mekinian, Arsene; Koster, Matthew; Coelho, Henrique; Fossard, Gaelle; Barraco, Fiorenza; Galicier, Lionel; Bienvenu, Boris; Hirsch, Pierre; Vial, Guillaume; Boutin, Anne Blandine; Le Guenno, Guillaume; Bigot, Adrien; Warrington, Kenneth; Kermani, Tanaz; Jamilloux, Yvan; Grayson, Peter C.; Patel, Bhavisha A.; Beck, David B.; Fenaux, Pierre; Sujobert, Pierre; ...More
PUBLISHED: 2021, SOURCE: BLOOD, VOLUME: 138
INDEXED IN: WOS
5
TITLE: Achievement of red blood cell transfusion independence in red blood cell transfusion-dependent patients with lower-risk non-del(5q) myelodysplastic syndromes correlates with serum erythropoietin levels  Full Text
AUTHORS: Valeria Santini; Antonio Almeida; Aristoteles Giagounidis; Barry Skikne; Beach, CL; Jerry Weaver; Nora Tu; Pierre Fenaux;
PUBLISHED: 2020, SOURCE: LEUKEMIA & LYMPHOMA, VOLUME: 61, ISSUE: 6
INDEXED IN: Scopus WOS
6
TITLE: Impact of red blood cell transfusion dose density on progression-free survival in patients with lower-risk myelodysplastic syndromes  Full Text
AUTHORS: Louise de Swart; Simon Crouch; Marlijn Hoeks; Alex Smith; Saskia Langemeijer; Pierre Fenaux; Argiris Symeonidis; Jaroslav Cermak; Eva Hellstrom Lindberg; Reinhard Stauder; Guillermo Sanz; Moshe Mittelman; Mette Skov Holm; Luca Malcovati; Krzysztof Madry; Ulrich Germing; Aurelia Tatic; Aleksandar Savic; Antonio Medina Almeida; Njetocka Gredelj Simec; Agnes Guerci Bresler; Odile Beyne Rauzy; Dominic Culligan; Ioannis Kotsianidis; Raphael Itzykson; Corine van Marrewijk; Nicole Blijlevens; David Bowen; Theo de Witte; ...More
PUBLISHED: 2020, SOURCE: HAEMATOLOGICA, VOLUME: 105, ISSUE: 3
INDEXED IN: Scopus WOS
7
TITLE: Impact of treatment with iron chelation therapy in patients with lower-risk myelodysplastic syndromes participating in the European MDS registry  Full Text
AUTHORS: Marlijn Hoeks; Ge Yu; Saskia Langemeijer; Simon Crouch; Louise de Swart; Pierre Fenaux; Argiris Symeonidis; Jaroslav Cermak; Eva Hellstrom Lindberg; Guillermo Sanz; Reinhard Stauder; Mette Skov Holm; Moshe Mittelman; Krzysztof Madry; Luca Malcovati; Aurelia Tatic; Antonio Medina Almeida; Ulrich Germing; Aleksandar Savic; Njetocka Gredelj Simec; Dominic Culligan; Raphael Itzykson; Agnes Guerci Bresler; Borhane Slama; Arjan van de Loosdrecht; Corine van Marrewijk; Jackie Droste; Nicole Blijlevens; Marian van Kraaij; David Bowen; Theo de Witte; Alex Smith; ...More
PUBLISHED: 2020, SOURCE: HAEMATOLOGICA, VOLUME: 105, ISSUE: 3
INDEXED IN: WOS
8
TITLE: Impact of somatic mutations on response to lenalidomide in lower-risk non-del(5q) myelodysplastic syndromes patients
AUTHORS: Valeria Santini; Pierre Fenaux; Aristoteles Giagounidis; Uwe Platzbecker; Alan F List; Torsten Haferlach; Jim Zhong; Chengqing Q Wu; Konstantinos Mavrommatis; Beach, CL; Kyle J MacBeth; Antonio Almeida;
PUBLISHED: 2020, SOURCE: LEUKEMIA
INDEXED IN: Scopus WOS
9
TITLE: Guideline-based indicators for adult patients with myelodysplastic syndromes
AUTHORS: Kristina Stojkov; Tobias Silzle; Georg Stussi; David Schwappach; Juerg Bernhard; David Bowen; Jaroslav Cermak; Avinash G Dinmohamed; Corien Eeltink; Sabrina Eggmann; Pierre Fenaux; Ulrich Germing; Manuel Haschke; Eva Hellstrom Lindberg; Monika Heger; Arjan A van de Loosdrecht; Jakob Passweg; Michael Pfeilstoecker; Uwe Platzbecker; Luca Malcovati; Antonio Medina de Almeida; Moshe Mittelman; Christine Morgenthaler; David P Steensma; Valeria Santini; Reinhard Stauder; Argiris Symeonidis; Saemi Schaer; Charlotte Maddox; Theo de Witte; Julia Bohlius; Nicolas Bonadies; ...More
PUBLISHED: 2020, SOURCE: BLOOD ADVANCES, VOLUME: 4, ISSUE: 16
INDEXED IN: Scopus WOS
10
TITLE: Novel dynamic outcome indicators and clinical endpoints in myelodysplastic syndrome; the European LeukemiaNet MDS Registry and MDS-RIGHT project perspective  Full Text
AUTHORS: Theo de Witte; Luca Malcovati; Pierre Fenaux; David Bowen; Argiris Symeonidis; Moshe Mittelman; Reinhard Stauder; Guillermo Sanz; Jaroslav Cermak; Saskia Langemeijer; Eva Hellstrom Lindberg; Ulrich Germing; Mette Skov Holm; Krzysztof Madry; Aurelia Tatic; Antonio Medina Almeida; Aleksandar Savic; Inga Mandac Rogulj; Raphael Itzykson; Marlijn Hoeks; Hege Gravdahl Garelius; Dominic Culligan; Ioannis Kotsianidis; Lionel Ades; Arjan A van de Loosdrecht; Corine van Marrewijk; Ge Yu; Simon Crouch; Alex Smith; ...More
PUBLISHED: 2020, SOURCE: HAEMATOLOGICA, VOLUME: 105, ISSUE: 11
INDEXED IN: Scopus WOS
Page 1 of 2. Total results: 18.