ProfileOfResearchers

TITLE: Nonclinical data supporting orphan medicinal product designations in the area of rare infectious diseases Full Text
AUTHORS: Maria E Sheean; Eva Malikova; Dinah Duarte; Giuseppe Capovilla; Laura Fregonese; Matthias P Hofer; Armando Magrelli; Segundo Mariz; Fernando Mendez Hermida; Robert Nistico; Tim Leest; Nikolaos V Sipsas; Stelios Tsigkos; Dinko Vitezic; Kristina Larsson; Bruno Sepodes; Violeta Stoyanova Beninska;
PUBLISHED: 2020, SOURCE: DRUG DISCOVERY TODAY, VOLUME: 25, ISSUE: 2

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Scopus

WOS

TITLE: Designation of orphan conditions in Europe: regulatory observations and considerations after implementation of regulation 141/2000
AUTHORS: Segundo Mariz; Kerstin Westermark; Bruno Sepodes;
PUBLISHED: 2020, SOURCE: EXPERT OPINION ON ORPHAN DRUGS, VOLUME: 8, ISSUE: 6

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Scopus

WOS

TITLE: Defining orphan conditions in the context of the European orphan regulation: challenges and evolution
AUTHORS: Daniel J O'Connor; Maria E Sheean; Matthias P Hofer; Stelios Tsigkos; Segundo Mariz; Laura Fregonese; Kristina Larsson; Virginie Hivert; Kerstin Westermark; Frauke Naumann Winter; Violeta Stoyanova Beninska; Ingeborg Barisic; Giuseppe Capovilla; Armando Magrelli; Bruno Sepodes;
PUBLISHED: 2019, SOURCE: NATURE REVIEWS DRUG DISCOVERY, VOLUME: 18, ISSUE: 7

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WOS

TITLE: Establishing rarity in the context of orphan medicinal product designation in the European Union Full Text
AUTHORS: Stelios Tsigkos; Matthias Philipp Hofer; Maria Elzbieta Sheean; Segundo Mariz; Kristina Larsson; Frauke Naumann Winter; Laura Fregonese; Bruno Sepodes;
PUBLISHED: 2018, SOURCE: DRUG DISCOVERY TODAY, VOLUME: 23, ISSUE: 3

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WOS

TITLE: Comparative analysis of the scope of European Union paediatric investigation plans with corresponding orphan designations
AUTHORS: Andrea Ecker; Segundo Mariz; Frauke Naumann Winter; Koenraad Norga; Ingeborg Barisic; Thomas Girard; Paolo Tomasi; Dirk Mentzer; Bruno Sepodes;
PUBLISHED: 2018, SOURCE: ARCHIVES OF DISEASE IN CHILDHOOD, VOLUME: 103, ISSUE: 5

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Scopus

WOS

TITLE: Evolving prevalence of haematological malignancies in orphan designation procedures in the European Union Full Text
AUTHORS: Benedetta Polsinelli; Stelios Tsigkos; Frauke Naumann Winter; Segundo Mariz; Bruno Sepodes;
PUBLISHED: 2017, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 12, ISSUE: 1

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Scopus

WOS

TITLE: The orphan drug pipeline in Europe
AUTHORS: Thomas Morel; Eline Picavet; Andre Lhoir; Jordi Llinares; Segundo Mariz; Bruno Sepodes; David Cassiman;
PUBLISHED: 2016, SOURCE: NATURE REVIEWS DRUG DISCOVERY, VOLUME: 15, ISSUE: 6

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WOS

TITLE: Worldwide collaboration for orphan drug designation
AUTHORS: Segundo Mariz; James H Reese; Kerstin Westermark; Lesley Greene; Takahiro Goto; Tatsuro Hoshino; Jordi Llinares Garcia; Bruno Sepodes;
PUBLISHED: 2016, SOURCE: NATURE REVIEWS DRUG DISCOVERY, VOLUME: 15, ISSUE: 6

INDEXED IN:

Scopus

WOS