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TITLE: Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy
AUTHORS: Coelho, Teresa; Marques, Wilson; Dasgupta, Noel R.; Chao, Chi Chao; Parman, Yesim; Franca, Marcondes Cavalcante; Guo, Yuh Cherng; Wixner, Jonas; Ro, Long Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington; Neuro ttransform Investigators; ...More
PUBLISHED: 2023, SOURCE: JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, VOLUME: 330, ISSUE: 15
INDEXED IN: Scopus WOS
2
TITLE: Optimal practices for the management of hereditary transthyretin amyloidosis: real-world experience from Japan, Brazil, and Portugal  Full Text
AUTHORS: Ando, Yukio; Waddington Cruz, Marcia; Sekijima, Yoshiki; Koike, Haruki; Ueda, Mitsuharu; Konishi, Hiroaki; Ishii, Tomonori; Coelho, Teresa;
PUBLISHED: 2023, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 18, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Guidelines and new directions in the therapy and monitoring of ATTRv amyloidosis
AUTHORS: Ando, Yukio; Adams, David; Benson, Merrill D.; Berk, John L.; Plante Bordeneuve, Violaine; Coelho, Teresa; Conceicao, Isabel; Ericzon, Bo Goran; Obici, Laura; Rapezz, Claudio; Sekijima, Yoshiki; Ueda, Mitsuharu; Palladini, Giovanni; Merlini, Giampaolo;
PUBLISHED: 2022, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
INDEXED IN: Scopus WOS
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TITLE: Characteristics of Patients with Hereditary Transthyretin Amyloidosis-Polyneuropathy (ATTRv-PN) in NEURO-TTRansform, an Open-label Phase 3 Study of Eplontersen
AUTHORS: Coelho, Teresa; Cruz, Marcia Waddington; Chao, Chi Chao; Parman, Yesim; Wixner, Jonas; Weiler, Markus; Barroso, Fabio A.; Dasgupta, Noel R.; Jung, Shiangtung W.; Schneider, Eugene; Viney, Nicholas J.; Dyck, P. James B.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Gertz, Morie A.; Obici, Laura; Berk, John L.;
PUBLISHED: 2022, SOURCE: NEUROLOGY AND THERAPY
INDEXED IN: Scopus WOS
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TITLE: Expert consensus recommendations to improve diagnosis of ATTR amyloidosis with polyneuropathy  Full Text
AUTHORS: David Adams; Yukio Ando; Joao Melo Beirao; Teresa Coelho; Morie A Gertz; Julian D Gillmore; Philip N Hawkins; Isabelle Lousada; Ole B Suhr; Giampaolo Merlini;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY
INDEXED IN: Scopus WOS
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TITLE: Avoiding misdiagnosis: expert consensus recommendations for the suspicion and diagnosis of transthyretin amyloidosis for the general practitioner  Full Text
AUTHORS: Morie Gertz; David Adams; Yukio Ando; Joao Melo Beirao; Sabahat Bokhari; Teresa Coelho; Raymond L Comenzo; Thibaud Damy; Sharmila Dorbala; Brian M Drachman; Marianna Fontana; Julian D Gillmore; Martha Grogan; Philip N Hawkins; Isabelle Lousada; Arnt V Kristen; Frederick L Ruberg; Ole B Suhr; Mathew S Maurer; Jose Nativi Nicolau; Candida Cristina Quarta; Claudio Rapezzi; Ronald Witteles; Giampaolo Merlini; ...More
PUBLISHED: 2020, SOURCE: BMC FAMILY PRACTICE, VOLUME: 21, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Guideline of transthyretin-related hereditary amyloidosis for clinicians  Full Text
AUTHORS: Yukio Ando; Teresa Coelho; John L Berk; Marcia Waddington Cruz; Bo Goran Ericzon; Shu ichi Ikeda; David D Lewis; Laura Obici; Violaine Plante Bordeneuve; Claudio Rapezzi; Gerard Said; Fabrizio Salvi;
PUBLISHED: 2013, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 8, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
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TITLE: Fibroblasts endocytose and degrade transthyretin aggregates in transthyretin-related amyloidosis
AUTHORS: Yohei Misumi; Yukio Ando; Nadia P Goncalves; Maria J Saraiva ;
PUBLISHED: 2013, SOURCE: LABORATORY INVESTIGATION, VOLUME: 93, ISSUE: 8
INDEXED IN: Scopus WOS CrossRef: 22
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TITLE: Immunization in familial amyloidotic polyneuropathy: counteracting deposition by immunization with a Y78F TTR mutant
AUTHORS: Terazaki, H; Ando, Y; Fernandes, R ; Yamamura, K; Maeda, S; Saraiva, MJ ;
PUBLISHED: 2006, SOURCE: LABORATORY INVESTIGATION, VOLUME: 86, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef: 35