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TITLE: Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model
AUTHORS: Burcu Bestas; Pedro M D Moreno; Emelie E M Blomberg; Dara K Mohammad; Amer F Saleh; Tolga Sutlu; Joel Z Nordin; Peter Guterstam; Manuela O Gustafsson; Shabnam Kharazi; Barbara Piatosa; Thomas C Roberts; Mark A Behlke; Matthew J A Wood; Michael J Gait; Karin E Lundin; Samir El Andaloussi; Robert Mansson; Anna Berglof; Jesper Wengel; Edvard I E Smith; ...More
PUBLISHED: 2014, SOURCE: JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 124, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef
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TITLE: Design of a peptide-based vector, PepFect6, for efficient delivery of siRNA in cell culture and systemically in vivo  Full Text
AUTHORS: Samir E L Andaloussi; Taavi Lehto; Imre Maeger; Katri Rosenthal Aizman; Iulian I Oprea; Oscar E Simonson; Helena Sork; Kariem Ezzat; Dana M Copolovici; Kaido Kurrikoff; Joana R Viola; Eman M Zaghloul; Rannar Sillard; Henrik J Johansson; Fatouma Said Hassane; Peter Guterstam; Julia Suhorutsenko; Pedro M D Moreno; Nikita Oskolkov; Jonas Haelldin; Ulf Tedebark; Andres Metspalu; Bernard Lebleu; Janne Lehtioe; Edvard I E Smith; Uelo Langel; ...More
PUBLISHED: 2011, SOURCE: NUCLEIC ACIDS RESEARCH, VOLUME: 39, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef
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TITLE: PepFect 14, a novel cell-penetrating peptide for oligonucleotide delivery in solution and as solid formulation  Full Text
AUTHORS: Kariem Ezzat; Samir EL Andaloussi; Eman M Zaghloul; Taavi Lehto; Staffan Lindberg; Pedro M D Moreno; Joana R Viola; Tarek Magdy; Rania Abdo; Peter Guterstam; Rannar Sillard; Suzan M Hammond; Matthew J A Wood; Andrey A Arzumanov; Michael J Gait; Edvard I E Smith; Mattias Hallbrink; Ulo Langel;
PUBLISHED: 2011, SOURCE: NUCLEIC ACIDS RESEARCH, VOLUME: 39, ISSUE: 12
INDEXED IN: Scopus WOS CrossRef