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TITLE: Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model
AUTHORS: Burcu Bestas; Pedro M D Moreno; Emelie E M Blomberg; Dara K Mohammad; Amer F Saleh; Tolga Sutlu; Joel Z Nordin; Peter Guterstam; Manuela O Gustafsson; Shabnam Kharazi; Barbara Piatosa; Thomas C Roberts; Mark A Behlke; Matthew J A Wood; Michael J Gait; Karin E Lundin; Samir El Andaloussi; Robert Mansson; Anna Berglof; Jesper Wengel; Edvard I E Smith; ...More
PUBLISHED: 2014, SOURCE: JOURNAL OF CLINICAL INVESTIGATION, VOLUME: 124, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef