1
TITLE: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTHORS: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 3
INDEXED IN: Scopus WOS
2
TITLE: Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis  Full Text
AUTHORS: Teresa Coelho; Aaron Yarlas; Marcia Waddington Cruz; Michelle K White; Asia Sikora Kessler; Andrew Lovley; Michael Pollock; Spencer Guthrie; Elizabeth J Ackermann; Steven G Hughes; Chafic Karam; Sami Khella; Morie Gertz; Giampaolo Merlini; Laura Obici; Hartmut H Schmidt; Michael Polydefkis; James J B Dyck; Thomas H Brannagan; Isabel Conceicao; Merrill D Benson; John L Berk; ...More
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 4
INDEXED IN: Scopus WOS
3
TITLE: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis (vol 264, pg 703, 2020)  Full Text
AUTHORS: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: JOURNAL OF NEUROLOGY, VOLUME: 267, ISSUE: 3
INDEXED IN: WOS
4
TITLE: Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTHORS: Laura Obici; John L Berk; Alejandra Gonzalez Duarte; Teresa Coelho; Julian Gillmore; Hartmut H J Schmidt; Matthias Schilling; Taro Yamashita; Celine Labeyrie; Thomas H Brannagan; Senda Ajroud Driss; Peter Gorevic; Arnt V Kristen; Jaclyn Franklin; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLISHED: 2020, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, VOLUME: 27, ISSUE: 3
INDEXED IN: Scopus WOS
5
TITLE: A phase II, open-label, extension study of long-term patisiran treatment in patients with hereditary transthyretin-mediated (hATTR) amyloidosis  Full Text
AUTHORS: Teresa Coelho; David Adams; Isabel Conceicao; Marcia Waddington Cruz; Hartmut H Schmidt; Juan Buades; Josep Campistol; John L Berk; Michael Polydefkis; Jing Jing Wang; Jihong H Chen; Marianne T Sweetser; Jared Gollob; Ole B Suhr;
PUBLISHED: 2020, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 15, ISSUE: 1
INDEXED IN: Scopus WOS
6
TITLE: "Red-flag" symptom clusters in transthyretin familial amyloid polyneuropathy  Full Text
AUTHORS: Isabel Conceicao; Alejandra Gonzalez Duarte; Laura Obici; Hartmut H J Schmidt; Damien Simoneau; Moh Lim Ong; Leslie Amass;
PUBLISHED: 2016, SOURCE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 21, ISSUE: 1
INDEXED IN: WOS
7
TITLE: Management of asymptomatic gene carriers of transthyretin familial amyloid polyneuropathy. TTR-FAP Gene Carriers  Full Text
AUTHORS: Hartmut H J Schmidt; Fabio Barroso; Alejandra Gonzalez Duarte; Isabel Conceicao; Laura Obici; Denis Keohane; Leslie Amass;
PUBLISHED: 2016, SOURCE: MUSCLE & NERVE, VOLUME: 54, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef
8
TITLE: PATISIRAN PH 2 OPEN-LABEL EXTENSION STUDY IN FAMILIAL AMYLOIDOTIC POLYNEUROPATHY
AUTHORS: Hartmut Schmidt; David Adams; Teresa Coelho; Isabel Conceicao; Marcia Waddington Cruz; Juan Buades; Josep Campistol; Jean Pouget; Jared Gollob; Ole Suhr;
PUBLISHED: 2016, SOURCE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 87, ISSUE: 12
INDEXED IN: WOS
9
TITLE: Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis  Full Text
AUTHORS: Morie A Gertz; Merrill D Benson; Peter J Dyck; Martha Grogan; Terresa Coelho; Marcia Cruz; John L Berk; Violaine Plante Bordeneuve; Hartmut H J Schmidt; Giampaolo Merlini;
PUBLISHED: 2015, SOURCE: JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, VOLUME: 66, ISSUE: 21
INDEXED IN: WOS CrossRef
10
TITLE: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTHORS: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLISHED: 2015, SOURCE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, ISSUE: 11
INDEXED IN: WOS CrossRef
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