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TITLE: Characterization of Autosomal Dominant Hypercholesterolemia Caused by PCSK9 Gain of Function Mutations and Its Specific Treatment With Alirocumab, a PCSK9 Monoclonal Antibody
AUTHORS: Paul N Hopkins; Joep Defesche; Sigrid W Fouchier; Eric Bruckert; Gerald Luc; Bertrand Cariou; Barbara Sjouke; Trond P Leren; Mariko Harada Shiba; Hiroshi Mabuchi; Jean Pierre Rabes; Alain Carrie; Charles van Heyningen; Valerie Carreau; Michel Farnier; Yee P Teoh; Mafalda Bourbon; Masa aki Kawashiri; Atsushi Nohara; Handrean Soran; David D Marais; Hayato Tada; Marianne Abifadel; Catherine Boileau; Bernard Chanu; Shoji Katsuda; Ichiro Kishimoto; Gilles Lambert; Hisashi Makino; Yoshihiro Miyamoto; Matthieu Pichelin; Kunimasa Yagi; Masakazu Yamagishi; Yassine Zair; Scott Mellis; George D Yancopoulos; Neil Stahl; Johanna Mendoza; Yunling L Du; Sara Hamon; Michel Krempf; Gary D Swergold; ...More
PUBLISHED: 2015, SOURCE: CIRCULATION-CARDIOVASCULAR GENETICS, VOLUME: 8, ISSUE: 6
INDEXED IN: WOS CrossRef