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TITLE: Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
AUTHORS: Benson, MD; Waddington Cruz, M; Berk, JL; Polydefkis, M; Dyck, PJ; Wang, AK; Plante Bordeneuve, V; Barroso, FA; Merlini, G; Obici, L; Scheinberg, M; Brannagan, TH; Litchy, WJ; Whelan, C; Drachman, BM; Adams, D; Heitner, SB; Conceicao, I; Schmidt, HH; Vita, G; Campistol, JM; Gamez, J; Gorevic, PD; Gane, E; Shah, AM; Solomon, SD; Monia, BP; Hughes, SG; Kwoh, TJ; McEvoy, BW; Jung, SW; Baker, BF; Ackermann, EJ; Gertz, MA; Coelho, T; ...More
PUBLISHED: 2018, SOURCE: NEW ENGLAND JOURNAL OF MEDICINE, VOLUME: 379, ISSUE: 1
INDEXED IN: Scopus WOS