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TITLE: Tafamidis polyneuropathy amelioration requires modest increases in transthyretin stability even though increases in plasma native TTR and decreases in non-native TTR do not predict response  Full Text
AUTHORS: Monteiro, Cecilia; Mesgarzadeh, Jaleh S.; Anselmo, Joao; Fernandes, Joana; Novais, Marta; Rodrigues, Carla; Powers, David L.; Powers, Evan T.; Coelho, Teresa; Kelly, Jeffery W.;
PUBLISHED: 2022, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
INDEXED IN: Scopus WOS
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TITLE: Cerebrospinal fluid and vitreous body exposure to orally administered tafamidis in hereditary ATTRV30M (p.TTRV50M) amyloidosis patients
AUTHORS: Cecilia Monteiro; Ana Martins da Silva; Natalia Ferreira; Jaleh Mesgarzadeh; Marta Novais; Teresa Coelho; Jeffery W Kelly;
PUBLISHED: 2018, SOURCE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, VOLUME: 25, ISSUE: 2
INDEXED IN: WOS