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TITLE: THE RCT223 NANOCORRECTOR RESTORES FUNCTION IN PRIMARY HBE CELLS DERIVED FROM CYSTIC FIBROSIS PATIENTS WITH NONSENSE MUTATIONS
AUTHORS: Torres, MJ; Devulapally, R; Coquelin, MI; Miller, J; Millen, L; De Keyzer, L; Cai, Z; Li, Q; Wangen, J; Harrington, J; Patel P Thakerar; Oliveira, C; Sheppard, DN; Feranchak, A; Green, R; Bihler, H; Mense, M; Bridges, RJ; Thomas, PJ; Siegwart, D; Johnson, AE; ...More
PUBLISHED: 2019, SOURCE: PEDIATRIC PULMONOLOGY, VOLUME: 54
INDEXED IN: WOS