2
TITLE: Systems Approaches to Unravel Molecular Function: High-content siRNA Screen Identifies TMEM16A Traffic Regulators as Potential Drug Targets for Cystic Fibrosis  Full Text
AUTHORS: Pinto, Madalena C.; Botelho, Hugo M.; Silva, Iris A. L.; Railean, Violeta; Neumann, Beate; Pepperkok, Rainer; Schreiber, Rainer; Kunzelmann, Karl; Amaral, Margarida D.;
PUBLISHED: 2022, SOURCE: JOURNAL OF MOLECULAR BIOLOGY, VOLUME: 434, ISSUE: 5
INDEXED IN: Scopus WOS
3
TITLE: Exploring YAP1-centered networks linking dysfunctional CFTR to epithelial-mesenchymal transition
AUTHORS: Quaresma, Margarida C.; Botelho, Hugo M.; Pankonien, Ines; Rodrigues, Claudia S.; Pinto, Madalena C.; Costa, Pau R.; Duarte, Aires; Amaral, Margarida D.;
PUBLISHED: 2022, SOURCE: LIFE SCIENCE ALLIANCE, VOLUME: 5, ISSUE: 9
INDEXED IN: Scopus WOS
5
TITLE: Absence of EPAC1 Signaling to Stabilize CFTR in Intestinal Organoids  Full Text
AUTHORS: Ferreira, Joao F.; Silva, Iris A. L.; Botelho, Hugo M.; Amaral, Margarida D.; Farinha, Carlos M.;
PUBLISHED: 2022, SOURCE: CELLS, VOLUME: 11, ISSUE: 15
INDEXED IN: Scopus WOS
6
TITLE: A Drug Screening Reveals Minocycline Hydrochloride as a Therapeutic Option to Prevent Breast Cancer Cells Extravasation across the Blood-Brain Barrier
AUTHORS: Godinho Pereira, Joana; Lopes, Margarida Dionisio; Garcia, Ana Rita; Botelho, Hugo M.; Malho, Rui; Figueira, Ines; Brito, Maria Alexandra;
PUBLISHED: 2022, SOURCE: BIOMEDICINES, VOLUME: 10, ISSUE: 8
INDEXED IN: Scopus WOS
7
TITLE: CFTR processing, trafficking and interactions  Full Text
AUTHORS: Margarida D Amaral; Darren M Hutt; Valeria Tomati; Hugo M Botelho; Nicoletta Pedemonte;
PUBLISHED: 2020, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 19
INDEXED IN: Scopus WOS
8
TITLE: Full Rescue of F508del-CFTR Processing and Function by CFTR Modulators Can Be Achieved by Removal of Two Regulatory Regions  Full Text
AUTHORS: Inna Uliyakina; Hugo M Botelho; Ana C da Paula; Sara Afonso; Miguel J Lobo; Veronica Felicio; Carlos M Farinha; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 21, ISSUE: 12
INDEXED IN: Scopus WOS
9
TITLE: Organoids as a personalized medicine tool for ultra-rare mutations in cystic fibrosis: The case of S955P and 1717-2A > G  Full Text
AUTHORS: Iris A L Silva; Tereza Dousova; Sofia Ramalho; Raquel Centeio; Luka A Clarke; Violeta Railean; Hugo M Botelho; Andrea Holubova; Iveta Valaskova; Jiunn Tyng Yeh; Tzyh Chang Hwang; Carlos M Farinha; Karl Kunzelmann; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: BIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR BASIS OF DISEASE, VOLUME: 1866, ISSUE: 11
INDEXED IN: Scopus WOS
10
TITLE: An open-source high-content analysis workflow for CFTR function measurements using the forskolin-induced swelling assay  Full Text
AUTHORS: Hagemeijer, MC; Vonk, AM; Awatade, NT; Silva, IAL; Tischer, C; Hilsenstein, V; Beekman, JM; Amaral, MD; Botelho, HM;
PUBLISHED: 2020, SOURCE: BIOINFORMATICS, VOLUME: 36, ISSUE: 24
INDEXED IN: Scopus WOS
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