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TITLE: Global reach of over 20 years of experience in the patient-centered Fabry Registry: Advancement of Fabry disease expertise and dissemination of real-world evidence to the Fabry community  Full Text
AUTHORS: Wanner, Christoph; Ortiz, Alberto; Wilcox, William R.; Hopkin, Robert J.; Johnson, Jack; Ponce, Elvira; Ebels, Johan T.; Batista, Julie L.; Maski, Manish; Politei, Juan M.; Martins, Ana Maria; Banikazemi, Maryam; Linhart, Ales; Mauer, Michael; Oliveira, JP; Weidemann, Frank; Germain, Dominique P.;
PUBLISHED: 2023, SOURCE: MOLECULAR GENETICS AND METABOLISM, VOLUME: 139, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef