Navigating the Orphan Medicinal Product Designation: Evidence Requirements for Gene Therapies in Europe

AuthID
P-017-F31
13
Author(s)
Palomo, GM
·
Pose Boirazian, T
·
Naumann Winter, F
·
Costa, E
·
Duarte, DM
·
Kalland, ME
·
Malikova, E
·
Matusevicius, D
·
Vitezic, D
·
Larsson, K
·
Magrelli, A
·
Stoyanova Beninska, V
·
Mariz, S
Document Type
Article
Year published
2025
Published
in MOLECULAR THERAPY, ISSN: 1525-0016
Volume: 33, Issue: 6, Pages: 2834-2841 (8)
Indexing
Publication Identifiers
Pubmed: 39489919
Scopus: 2-s2.0-85209114575
Wos: WOS:001505438600027
Source Identifiers
ISSN: 1525-0016
Export Publication Metadata
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