Availability, Accessibility and Delivery to Patients of the 28 Orphan Medicines Approved by the European Medicine Agency for Hereditary Metabolic Diseases in the Metabern Network

AuthID
P-00R-SKB
72
Author(s)
Heard, JM
·
Vrinten, C
·
Schlander, M
·
Bellettato, CM
·
van Lingen, C
·
Scarpa, M
·
Matthijs, G
·
Nassogne, MC
·
Debray, FG
·
Roland, D
·
[+52]·
Quelhas, D
·
Leao Teles, E
·
Azevedo, O
·
Silva, EMFR
·
Matos, LMDFD
·
Lajic, S
·
Darin, N
·
Groselj, U
·
Tansek, MZ
1
Group Author(s)
MetabERN Collaboration Grp
Document Type
Article
Year published
2020
Published
in ORPHANET JOURNAL OF RARE DISEASES, ISSN: 1750-1172
Volume: 15, Issue: 1
Indexing
Publication Identifiers
Pubmed: 31907071
Scopus: 2-s2.0-85077535952
Wos: WOS:000513719400001
Source Identifiers
ISSN: 1750-1172
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Name Order Name   Name Order Name   Name Order Name
1 Heard, JM;   2 Vrinten, C;   3 Schlander, M;
4 Bellettato, CM;   5 van Lingen, C;   6 Scarpa, M;
7 Matthijs, G;   8 Nassogne, MC;   9 Debray, FG;
10 Roland, D;   11 Chamova, T;   12 Kozich, V;
13 Pavel, J;   14 Zenker, M;   15 Lampe, C;
16 Das, AM;   17 Hennermann, J;   18 Kolker, S;
19 Weinhold, N;   20 Mohnike, K;   21 Gruenert, S;
22 Lund, AM;   23 Morales Conejo, M;   24 del Toro Riera, M;
25 Aldamiz Echevarria, L;   26 Garcia Silva, MT;   27 Schiff, M;
28 Gouya, L;   29 Labrune, P;   30 de Lonlay, P;
31 Belmatoug, N;   32 Germain, DP;   33 Cano, A;
34 Dobbelaere, D;   35 Jones, S;   36 Dawson, C;
37 Deegan, P;   38 Santra, S;   39 Vijay, S;
40 Ramadza, DP;   41 Baric, I;   42 Zigman, T;
43 Pflieger, G;   44 Szakszon, K;   45 Kaposta, R;
46 Gasperini, S;   47 Burlina, A;   48 Parenti, G;
49 Strisciuglio, P;   50 Ceccarini, G;   51 Federico, A;
52 Simonati, A;   53 Tumiene, B;   54 Huidekoper, H;
55 van Spronsen, F;   56 Bosch, A;   57 Rubio Gozalbo, ME;
58 Visser, G;   59 Tangeraas, T;   60 Aarsand, A;
61 Kiec Wilk, B;   62 Gaspar, AMSM;   63 Quelhas, D;
64 Leao Teles, E;   65 Azevedo, O;   66 Silva, EMFR;
67 Matos, LMDFD;   68 Martins, E ;   69 Lajic, S;
70 Darin, N;   71 Groselj, U;   72 Tansek, MZ;