Stable or Improved Neurological Manifestations During Miglustat Therapy in Patients from the International Disease Registry for Niemann-Pick Disease Type C: An Observational Cohort Study

AuthID
P-00T-47Q
199
Author(s)
Patterson, MC
·
Mengel, E
·
Vanier, MT
·
Schwierin, B
·
Muller, A
·
Cornelisse, P
·
Pineda, M
·
Amado Fondo, A
·
Amraoui, Y
·
Andria, G
·
[+96]·
[+83]·
Widner, H
·
Wilcke, C
·
Wildish, L
·
Wraith, E
·
Wright, N
·
Xaidara, A
·
Yamamoto, M
·
Zallocco, F
·
Zielke, S
Document Type
Article
Year published
2015
Published
in Orphanet Journal of Rare Diseases, ISSN: 1750-1172
Volume: 10, Issue: 1
Indexing
Publication Identifiers
Pubmed: 26017010
Scopus: 2-s2.0-84931039342
Source Identifiers
ISSN: 1750-1172
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Name Order Name   Name Order Name   Name Order Name
1 Patterson, MC;   2 Mengel, E;   3 Vanier, MT;
4 Schwierin, B;   5 Muller, A;   6 Cornelisse, P;
7 Pineda, M;   8 Amado Fondo, A;   9 Amraoui, Y;
10 Andria, G;   11 Arellano, M;   12 Audoin, B;
13 Azcona, C;   14 Barr, C;   15 Baruteau, J;
16 Baumgartner, C;   17 Bell, L;   18 Bembi, B;
19 Benneddif, K;   20 Bernard, G;   21 Bobocea, N;
22 Bodzioch, M;   23 Boettcher, T;   24 Bonnan, M;
25 Broue, P;   26 Bruni, A;   27 Caceres, M;
28 Camino, R;   29 Campbell, E;   30 Cances, C;
31 Cannell, P;   32 Cesar, J;   33 Chabrol, B;
34 Chakrapani, A;   35 Colao, R;   36 Collet, A;
37 Corsetti, T;   38 Cousins, A;   39 Covanis, A;
40 Cox, T;   41 Cuisset, JM;   42 Dardis, A;
43 Das, A;   44 Deegan, P;   45 Dengler, T;
46 Deodato, F;   47 Derralynn, H;   48 Di Donato, I;
49 Di Rocco, M;   50 Dinopoulos, A;   51 Pakiela, D;
52 Eckehard, S;   53 Engelen, M;   54 Eyer, D;
55 Fecarotta, S;   56 Federico, A;   57 Filla, A;
58 Fiumara, A;   59 Fonseca, MJ;   60 Gabrielli, O;
61 Garcia, T;   62 Garrote, J;   63 Gissen, P;
64 Giugliani, L;   65 Greenberg, C;   66 Heron, B;
67 Hertzberg, C;   68 Higgins, F;   69 Hill, A;
70 Hiwot, T;   71 Hlavata, A;   72 Hörbe Blindt, A;
73 Howley, E;   74 Hussain, N;   75 Illsinger, S;
76 Imrie, J;   77 Jacklin, E;   78 Jones, S;
79 Jovanovic, A;   80 Kaczmarek, V;   81 Kaphan, E;
82 Kibaek, M;   83 Kleinhans, P;   84 Klünemann, KH;
85 Koch, SM;   86 Koegl Wallner, W;   87 Kolnikova, M;
88 Korenke, GC;   89 Korinthenberg, R;   90 Kumari, S;
91 Lachmann, R;   92 Lee Ann, L;   93 Likopoulou, L;
94 Lilienthal, E;   95 Link, B;   96 Lippold, M;
97 Lopez Laso, E;   98 Luecke, T;   99 Lundgren, J;
100 Mackrell, M;   101 Madruga, M;   102 Maletta, R;
103 Malinova, V;   104 Manners, J;   105 Marinei, R;
106 Marquardt, T;   107 Martins, E ;   108 Martins, AM;
109 Martins, N;   110 McAlister, L;   111 McCabe, A;
112 McKie, M;   113 McMahon, S;   114 Meehan, M;
115 Meldgaard Lund, A;   116 Mendozah, C;   117 Meyer, A;
118 Mielke, S;   119 Milligan, A;   120 Mir, P;
121 Moisa, M;   122 Mombelli, C;   123 Morris, L;
124 Müller Vom Hagen, J;   125 Munoz, B;   126 Murphy, E;
127 Nagarajan, L;   128 Neto, PB;   129 Nevsimalova, S;
130 Nia, S;   131 Nicolai, J;   132 Niemann, D;
133 Niktari, G;   134 O'Callaghan, MDM;   135 Paucar Arce, M;
136 Peers, K;   137 Peintinger, L;   138 Peralta, M;
139 Pérez, J;   140 Perez Poyato, M;   141 Petrariu, A;
142 Puschmann, A;   143 Raiman, J;   144 Rask, O;
145 Rataj, J;   146 Raymond Gaynor, C;   147 Reichelt, G;
148 Ribeiro, E;   149 Riches, V;   150 Roberts, A;
151 Roelants, J;   152 Rohrbach, M;   153 Rokicki, D;
154 Rolfs, A;   155 Russo, C;   156 Rutsch, F;
157 Saleem, R;   158 Santos, M;   159 Schmutz, P;
160 Schwahn, B;   161 Sedel, F;   162 Semotok, J;
163 Sharma, R;   164 Silska, S;   165 Silva, A;
166 Simmons, L;   167 Sivera, R;   168 Skorpen, J;
169 Sole, G;   170 Souza, C;   171 Stadlober Degwerth, M;
172 Starling, J;   173 Temudo, T;   174 Tomas, M;
175 Tranchant, C;   176 Uziel, G;   177 Valayannopoulous, V;
178 Van Den Hout, H;   179 Van Der Tol, L;   180 Van Spronsen, F;
181 Vellodi, A;   182 Verdu, A;   183 Vilchez, JJ;
184 Vinaixa, A;   185 Visser, G;   186 Voelker, J;
187 Waldek, S;   188 Walter, A;   189 Walterfang, M;
190 Wein, U;   191 Widner, H;   192 Wilcke, C;
193 Wildish, L;   194 Wraith, E;   195 Wright, N;
196 Xaidara, A;   197 Yamamoto, M;   198 Zallocco, F;
199 Zielke, S;