Standardising Clinical Outcomes Measures for Adult Clinical Trials in Fabry Disease: A Global Delphi Consensus

AuthID
P-00T-K0T
34
Author(s)
Moreno Martinez, D
·
Aguiar, P
·
Auray Blais, C
·
Beck, M
·
Burlina, A
·
Cole, D
·
Elliott, P
·
Feldt Rasmussen, U
·
Feriozzi, S
·
[+11]·
[+3]·
Rozenfeld, P
·
Schiffmann, R
·
Svarstad, E
·
Talbot, AS
·
Thomas, M
·
Tondel, C
·
Warnock, D
·
West, ML
·
Hughes, DA
Document Type
Article
Year published
2021
Published
in MOLECULAR GENETICS AND METABOLISM, ISSN: 1096-7192
Volume: 132, Issue: 4, Pages: 234-243 (10)
Indexing
Publication Identifiers
Pubmed: 33642210
Scopus: 2-s2.0-85101623383
Wos: WOS:000631172600005
Source Identifiers
ISSN: 1096-7192
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Name Order Nome   Name Order Nome   Name Order Nome
1 Moreno Martinez, D;   2 Aguiar, P;   3 Auray Blais, C;
4 Beck, M;   5 Bichet, DG;   6 Burlina, A;
7 Cole, D;   8 Elliott, P;   9 Feldt Rasmussen, U;
10 Feriozzi, S;   11 Fletcher, J;   12 Giugliani, R;
13 Jovanovic, A;   14 Kampmann, C;   15 Langeveld, M;
16 Lidove, O;   17 Linhart, A;   18 Mauer, M;
19 Moon, JC;   20 Muir, A;   21 Nowak, A;
22 Oliveira, JP;   23 Ortiz, A;   24 Pintos Morell, G;
25 Politei, J;   26 Rozenfeld, P;   27 Schiffmann, R;
28 Svarstad, E;   29 Talbot, AS;   30 Thomas, M;
31 Tondel, C;   32 Warnock, D;   33 West, ML;
34 Hughes, DA;