1
TITLE: Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease
AUTHORS: Biegstraaten, M; Cox, TM; Belmatoug, N; Berger, MG; Collin Histed, T; Vom Dahl, SV; Di Rocco, M; Fraga, C; Giona, F; Giraldo, P; Hasanhodzic, M; Hughes, DA; Iversen, PO; Kiewiet, AI; Lukina, E; Machaczka, M; Marinakis, T; Mengel, E; Pastores, GM; Ploeckinger, U; Rosenbaum, H; Serratrice, C; Symeonidis, A; Szer, J; Timmerman, J; Tylki Szymanska, A; Weisz W Hubshman; Zafeiriou, DI; a Zimran; Hollak, CEM; ...More
PUBLISHED: 2018, SOURCE: BLOOD CELLS MOLECULES AND DISEASES, VOLUME: 68
INDEXED IN: WOS
2
TITLE: Management and monitoring recommendations for the use of eliglustat in adults with type 1 Gaucher disease in Europe  Full Text
AUTHORS: Nadia Belmatoug; Maja Di Rocco; Cristina Fraga; Pilar Giraldo; Derralynn Hughes; Elena Lukina; Pierre Maison Blanche; Martin Merkel; Claus Niederau; Ursula Plockinger; Johan Richter; Thomas M Stulnig; Stephan vom Dahl; Timothy M Cox;
PUBLISHED: 2017, SOURCE: EUROPEAN JOURNAL OF INTERNAL MEDICINE, VOLUME: 37
INDEXED IN: WOS
3
TITLE: Force Majeure: Therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease  Full Text
AUTHORS: Carla E M Hollak; Stephan vom Dahl; Johannes M F G Aerts; Nadia Belmatoug; Bruno Bembi; Yossi Cohen; Tanya Collin Histed; Patrick Deegan; Laura van Dussen; Pilar Giraldo; Eugen Mengel; Helen Michelakakis; Jeremy Manuel; Martin Hrebicek; Rosella Parini; Joerg Reinke; Maja di Rocco; Miguel Pocovi; Maria Clara S Sa Miranda ; Anna Tylki Szymanska; Ari Zimran; Timothy M Cox; ...More
PUBLISHED: 2010, SOURCE: BLOOD CELLS MOLECULES AND DISEASES, VOLUME: 44, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef