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TITLE: Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy
AUTHORS: Jacqueline Corrigan Curay; Odile Cohen Haguenauer; Marina O'Reilly; Susan R Ross; Hung Fan; Naomi Rosenberg; Nikunj Somia; Nancy King; Theodore Friedmann; Cynthia Dunbar; Alessandro Aiuti; Luigi Naldini; Christopher Baum; Christof von Kalle; Hans Peter Kiem; Eugenio Montini; Frederic Bushman; Brian P Sorrentino; Manuel Carrondo ; Harry Malech; Gosta Gahrton; Robyn Shapiro; Linda Wolff; Eugene Rosenthal; Robert Jambou; John Zaia; Donald B Kohn; ...More
PUBLISHED: 2012, SOURCE: MOLECULAR THERAPY, VOLUME: 20, ISSUE: 6
INDEXED IN: Scopus WOS
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TITLE: Relevance of an Academic GMP Pan-European Vector Infra-Structure (PEVI)
AUTHORS: Cohen Haguenauer, O; Creff, N; Cruz, P; Tunc, C; Aiuti, A; Baum, C; Bosch, F; Blomberg, P; Cichutek, K; Collins, M; Danos, O; Dehaut, F; Federspiel, M; Galun, E; Garritsen, H; Hauser, H; Hildebrandt, M; Klatzmann, D; Merten, OW; Montini, E; O'Brien, T; Panet, A; Rasooly, L; Scherman, D; Schmidt, M; Schweizer, M; Tiberghien, P; Vandendriessche, T; Ziehr, H; Yla Herttuala, S; von Kalle, C; Gahrton, G; Carrondo, M ; ...More
PUBLISHED: 2010, SOURCE: CURRENT GENE THERAPY, VOLUME: 10, ISSUE: 6
INDEXED IN: Scopus WOS