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TITLE: Generation of a High Number of Healthy Erythroid Cells from Gene-Edited Pyruvate Kinase Deficiency Patient-Specific Induced Pluripotent Stem Cells
AUTHORS: Zita Garate; Oscar Quintana Bustamante; Ana M Crane; Emmanuel Olivier; Laurent Poirot; Roman Galetto; Penelope Kosinski; Collin Hill; Charles Kung; Xabi Agirre; Israel Orman; Laura Cerrato; Omaira Alberquilla; Fatima Rodriguez Fornes; Noemi Fusaki; Felix Garcia Sanchez; Tabita M Maia; Maria L Ribeiro; Julian Sevilla; Felipe Prosper; Shengfang F Jin; Joanne Mountford; Guillermo Guenechea; Agnes Gouble; Juan A Bueren; Brian R Davis; Jose C Segovia; ...More
PUBLISHED: 2015, SOURCE: STEM CELL REPORTS, VOLUME: 5, ISSUE: 6
INDEXED IN: Scopus WOS CrossRef