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TITLE: Bumetanide Oral Liquid Formulation for the Treatment of Children and Adolescents with Autism Spectrum Disorder: Design of Two Phase III Studies (SIGN Trials)  Full Text
AUTHORS: Veronique Crutel; Estelle Lambert; Pierre Francois Penelaud; Cristina Albarran Severo; Joaquin Fuentes; Antoine Rosier; Amaia Hervas; Stephane Marret; Guiomar Oliveira; Mara Parellada; Simon Kyaga; Sylvie Gouttefangeas; Marianne Bertrand; Denis Ravel; Bruno Falissard;
PUBLISHED: 2020, SOURCE: JOURNAL OF AUTISM AND DEVELOPMENTAL DISORDERS
INDEXED IN: Scopus WOS
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TITLE: The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts
AUTHORS: Dominique P Germain; Perry M Elliott; Bruno Falissard; Victor V Fomin; Max J Hilz; Ana Jovanovic; Ilkka Kantola; Ales Linhart; Renzo Mignani; Mehdi Namdar; Albina Nowak; Oliveira, JP ; Maurizio Pieroni; Miguel Viana Baptista; Christoph Wanner; Marco Spada;
PUBLISHED: 2019, SOURCE: MOLECULAR GENETICS AND METABOLISM REPORTS, VOLUME: 19
INDEXED IN: Scopus WOS CrossRef: 62