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TITLE: Simoctocog alfa (Nuwiq & REG;) in previously untreated patients with severe haemophilia A-Final efficacy and safety results from the NuProtect study  Full Text
AUTHORS: Mathias, Mary; Abraham, Aby; Belletrutti, Mark J.; Carcao, Manuel; Carvalho, Manuela; Chambost, Herve; Chan, Anthony K. C.; Dubey, Leonid; Ducore, Jonathan; Gattens, Michael; Gresele, Paolo; Gruel, Yves; Guillet, Benoit; Jimenez Yuste, Victor; Kitanovski, Lidija; Klukowska, Anna; Lohade, Sunil; Mancuso, Maria Elisa; Oldenburg, Johannes; Pollio, Berardino; Sigaud, Marianne; Vilchevska, Kateryna; Wu, John K. M.; Jansen, Martina; Belyanskaya, Larisa; Walter, Olaf; Knaub, Sigurd; Neufeld, Ellis J.; ...More
PUBLISHED: 2023, SOURCE: EUROPEAN JOURNAL OF HAEMATOLOGY
INDEXED IN: Scopus WOS
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TITLE: Novel manifestations of immune dysregulation and granule defects in gray platelet syndrome
AUTHORS: Matthew C Sims; Louisa Mayer; Janine H Collins; Tadbir K Bariana; Karyn Megy; Cecile Lavenu Bombled; Denis Seyres; Laxmikanth Kollipara; Frances S Burden; Daniel Greene; Dave Lee; Antonio Rodriguez Romera; Marie Christine Alessi; William J Astle; Wadie F Bahou; Loredana Bury; Elizabeth Chalmers; Rachael Da Silva; Erica De Candia; Sri V V Deevi; Samantha Farrow; Keith Gomez; Luigi Grassi; Andreas Greinacher; Paolo Gresele; Dan Hart; Marie Francoise Hurtaud; Anne M Kelly; Ron Kerr; Sandra Le Quellec; Thierry Leblanc; Eva B Leinoe; Rutendo Mapeta; Harriet McKinney; Alan D Michelson; Sara Morais; Diane Nugent; Sofia Papadia; Soo J Park; John Pasi; Gian Marco Podda; Man Chiu Poon; Rachel Reed; Mallika Sekhar; Hanna Shalev; Suthesh Sivapalaratnam; Orna Steinberg Shemer; Jonathan C Stephens; Robert C Tait; Ernest Turro; John K M Wu; Barbara Zieger; Taco W Kuijpers; Anthony D Whetton; Albert Sickmann; Kathleen Freson; Kate Downes; Wendy N Erber; Mattia Frontini; Paquita Nurden; Willem H Ouwehand; Remi Favier; Jose A Guerrero; ...More
PUBLISHED: 2020, SOURCE: BLOOD, VOLUME: 136, ISSUE: 17
INDEXED IN: Scopus WOS