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TITLE: Tau and neurofilament light-chain as fluid biomarkers in spinocerebellar ataxia type 3  Full Text
AUTHORS: Garcia Moreno, Hector; Prudencio, Mercedes; Thomas Black, Gilbert; Solanky, Nita; Jansen West, Karen R.; Hanna AL Shaikh, Rana; Heslegrave, Amanda; Zetterberg, Henrik; Santana, Magda M.; Pereira de Almeida, Luis; Vasconcelos Ferreira, Ana; Januario, Cristina; Infante, Jon; Faber, Jennifer; Klockgether, Thomas; Reetz, Kathrin; Raposo, Mafalda; Ferreira, Ana F.; Lima, Manuela; Schols, Ludger; Synofzik, Matthis; Hubener Schmid, Jeannette; Puschmann, Andreas; Gorcenco, Sorina; Wszolek, Zbigniew K.; Petrucelli, Leonard; Giunti, Paola; ...More
PUBLISHED: 2022, SOURCE: EUROPEAN JOURNAL OF NEUROLOGY
INDEXED IN: Scopus WOS
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TITLE: Toward allele-specific targeting therapy and pharmacodynamic marker for spinocerebellar ataxia type 3
AUTHORS: Mercedes Prudencio; Hector Garcia Moreno; Karen R Jansen West; Rana Hanna AL Shaikh; Tania F Gendron; Michael G Heckman; Matthew R Spiegel; Yari Carlomagno; Lillian M Daughrity; Yuping P Song; Judith A Dunmore; Natalie Byron; Bjorn Oskarsson; Katharine A Nicholson; Nathan P Staff; Sorina Gorcenco; Andreas Puschmann; Joao Lemos; Cristina Januario; Mark S LeDoux; Joseph H Friedman; James Polke; Robin Labrum; Vikram Shakkottai; Hayley S McLoughlin; Henry L Paulson; Takuya Konno; Osamu Onodera; Takeshi Ikeuchi; Mari Tada; Akiyoshi Kakita; John D Fryer; Christin Karremo; Ines Gomes; John N Caviness; Mark R Pittelkow; Jan Aasly; Ronald F Pfeiffer; Venka Veerappan; Eric R Eggenberger; William D Freeman; Josephine F Huang; Ryan J Uitti; Klaas J Wierenga; Iris Marin M Collazo; Philip W Tipton; Jay A van Gerpen; Marka van Blitterswijk; Guojun J Bu; Zbigniew K Wszolek; Paola Giunti; Leonard Petrucelli; ...More
PUBLISHED: 2020, SOURCE: SCIENCE TRANSLATIONAL MEDICINE, VOLUME: 12, ISSUE: 566
INDEXED IN: Scopus WOS