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TITLE: Extracellular vesicles-associated AAVs for the treatment of Machado-Joseph disease
AUTHORS: Henriques, Carina; Albuquerque, Patricia; Rufino Ramos, David; Lopes, Miguel M.; Leandro, Kevin; Miranda, Catarina O. ; Almeida, Rita; Lopes Gabriel, Guilherme; de Sousa Lourenco, Joao; Lopes, Sara M.; Gaspar, Laetitia S.; Lobo, Diana D.; Silva, Ana Carolina; Ribeiro Rodrigues, Teresa M.; Girao, Henrique; Gomes, Celia M.; Baganha, Rafael; Duarte, Sonia ; Maguire, Casey A.; Santana, Magda M.; de Almeida, Luis Pereira ; Nobre, Rui Jorge; ...More
PUBLISHED: 2026, SOURCE: MOLECULAR THERAPY, VOLUME: 34, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
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TITLE: Extracellular vesicles-mediated delivery of SpCas9 RNPs for therapeutic gene editing in Spinocerebellar Ataxia Type 3
AUTHORS: Leandro, Kevin; Rufino Ramos, David; Lopes, Sara M.; Silva, Francisca Santos; Paulo Rodrigues-Santos; Silva, Ana Carolina; Fernandes, Ana Rita; Henriques, Carina; Pereira, Dina; Lobo, Diana; Gabriel, Guilherme L.; Faro, Rosario; Nobre, Rui Jorge; Perdigao, Pedro R. L.; Kleinstiver, Benjamin P.; de Almeida, Luis Pereira ;
PUBLISHED: 2026, SOURCE: BIOMATERIALS, VOLUME: 331
INDEXED IN: WOS CrossRef
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TITLE: In Vitro Antiviral Activity of Red Algae Extracts from Chondracanthus teedei var. lusitanicus and Osmundea pinnatifida Against Coxsackievirus A12 and a Lentiviral Vector
AUTHORS: Santos Ferreira, Nanci; Nobrega, Clevio; Mota, Marta; Pereira de Almeida, Luis ; Pereira, Leonel; Goncalves, Teresa; Nogueira, Celia;
PUBLISHED: 2026, SOURCE: TROPICAL MEDICINE AND INFECTIOUS DISEASE, VOLUME: 11, ISSUE: 2
INDEXED IN: Scopus WOS CrossRef
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TITLE: AAV-mediated allele-specific silencing alleviates neuropathology in a novel non-human primate model of Spinocerebellar ataxia type 3
AUTHORS: Carina Henriques; Diana Duarte Lobo; Ana Carolina Silva; Ana Rita Fernandes; Miguel Monteiro Lopes; Audrey Fayard; Caroline Jan; Sophie Lecourtois; Martine Guillermier; Julien Flament; João Castelhano; Miguel Castelo-Branco; Rui Caetano Oliveira; Philippe Hantraye; Padmaja Yalamanchili; Steven de Marco; Romina Aron Badin; Luís Pereira de Almeida ; Rui Jorge Nobre;
PUBLISHED: 2025
INDEXED IN: CrossRef
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TITLE: Autophagy- and oxidative stress-related protein deregulation mediated by extracellular vesicles of human MJD/SCA3 iPSC-derived neuroepithelial stem cells and differentiated neural cultures  Full Text
AUTHORS: Mendonca, Liliana S.; Moreira, Ricardo; Henriques, Daniel; Zuzarte, Monica; Ribeiro Rodrigues, Teresa M.; Girao, Henrique; de Almeida, Luis Pereira ;
PUBLISHED: 2025, SOURCE: CELL DEATH & DISEASE, VOLUME: 16, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
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TITLE: Circadian rhythms are disrupted in patients and preclinical models of Machado-Joseph disease  Full Text
AUTHORS: Ribeiro, Rodrigo F. N.; Pereira, Dina; Lopes, Sara M.; Reis, Tiago; Silva, Patrick; Lobo, Diana D.; Gaspar, Laetitia S.; Duraes, Joao; Fernandes, Ana Rita; Ferreira Marques, Marisa; Carvalhas Almeida, Catarina; Peca, Joao; Alvaro, Ana Rita; Santana, Isabel; Santana, Magda M.; Silva, Maria Manuel C.; Pereira de Almeida, Luis ; Cavadas, Claudia ;
PUBLISHED: 2025, SOURCE: BRAIN, VOLUME: 148, ISSUE: 11
INDEXED IN: Scopus WOS CrossRef
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TITLE: Differential impact of mutant Ataxin-3 in hindbrain regions: further evidence of white matter loss as a core pathological feature  Full Text
AUTHORS: Henriques, Carina; Silva, Marta; Silva, Antonio; Rufino Ramos, David; Lopes, Miguel Monteiro; Badin, Romina Aron; Hantraye, Philippe; Almeida, Luis Pereira De ; Nobre, Rui Jorge;
PUBLISHED: 2025, SOURCE: EXPERIMENTAL NEUROLOGY, VOLUME: 393
INDEXED IN: Scopus WOS CrossRef: 1
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TITLE: Exosomes as Emerging Non-Invasive Biomarkers of Cervical Cancer: A Systematic Review and Meta-Analysis  Full Text
AUTHORS: Santos, Fernanda; Caramelo, Francisco A.; Tomaz, Jorge M. P.; Santana, Magda M.; Nobre, Rui J.; Almeida, Luis P. ; Figueiredo Dias, Margarida;
PUBLISHED: 2025, SOURCE: CANCERS, VOLUME: 17, ISSUE: 24
INDEXED IN: Scopus WOS CrossRef: 1
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TITLE: Exploring TLR agonists as adjuvants for COVID-19 oral vaccines  Full Text
AUTHORS: Felix, Paulo; Melo, Alexandra A.; Costa, Joao Panao; Colaco, Mariana; Pereira, Dina; Nunez, Jisette; de Almeida, Luis Pereira ; Borges, Olga;
PUBLISHED: 2025, SOURCE: VACCINE, VOLUME: 53
INDEXED IN: Scopus WOS CrossRef
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