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TITLE: Development of novel therapeutics for all individuals with CF (the future goes on)  Full Text
AUTHORS: Amaral, Margarida D.; Harrison, Patrick T.;
PUBLISHED: 2023, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 22
INDEXED IN: Scopus WOS
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TITLE: Identification of novel F508del-CFTR traffic correctors among triazole derivatives  Full Text
AUTHORS: Bacalhau, Mafalda; Ferreira, Filipa C.; Kmit, Arthur; Souza, Felipe R.; da Silva, Veronica D.; Pimentel, Andre S.; Amaral, Margarida D.; Buarque, Camilla D.; Lopes Pacheco, Miqueias;
PUBLISHED: 2023, SOURCE: EUROPEAN JOURNAL OF PHARMACOLOGY, VOLUME: 938
INDEXED IN: Scopus WOS
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TITLE: Additive Potentiation of R334W-CFTR Function by Novel Small Molecules
AUTHORS: Bacalhau, Mafalda; Ferreira, Filipa C.; Silva, Iris A. L.; Buarque, Camilla D.; Amaral, Margarida D.; Lopes Pacheco, Miqueias;
PUBLISHED: 2023, SOURCE: JOURNAL OF PERSONALIZED MEDICINE, VOLUME: 13, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: What Can RNA-Based Therapy Do for Monogenic Diseases?  Full Text
AUTHORS: Clarke, Luka A.; Amaral, Margarida D.;
PUBLISHED: 2023, SOURCE: PHARMACEUTICS, VOLUME: 15, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Mutation-class dependent signatures outweigh disease-associated processes in cystic fibrosis cells  Full Text
AUTHORS: Santos, Lucia; Nascimento, Rui; Duarte, Aires; Railean, Violeta; Amaral, Margarida D. D.; Harrison, Patrick T. T.; Gama Carvalho, Margarida; Farinha, Carlos M. M.;
PUBLISHED: 2023, SOURCE: CELL AND BIOSCIENCE, VOLUME: 13, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Development of novel therapeutics for all individuals with CF (the future goes on)  Full Text
AUTHORS: Amaral, Margarida D.; Harrison, Patrick T.;
PUBLISHED: 2023, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 22
INDEXED IN: WOS
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TITLE: Rescue of Mutant CFTR Trafficking Defect by the Investigational Compound MCG1516A  Full Text
AUTHORS: Lopes Pacheco, M; Bacalhau, M; Ramalho, SS; Silva, IAL; Ferreira, FC; Carlile, GW; Thomas, DY; Farinha, CM; Hanrahan, JW; Amaral, MD;
PUBLISHED: 2022, SOURCE: CELLS, VOLUME: 11, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Systems Approaches to Unravel Molecular Function: High-content siRNA Screen Identifies TMEM16A Traffic Regulators as Potential Drug Targets for Cystic Fibrosis  Full Text
AUTHORS: Pinto, Madalena C.; Botelho, Hugo M.; Silva, Iris A. L.; Railean, Violeta; Neumann, Beate; Pepperkok, Rainer; Schreiber, Rainer; Kunzelmann, Karl; Amaral, Margarida D.;
PUBLISHED: 2022, SOURCE: JOURNAL OF MOLECULAR BIOLOGY, VOLUME: 434, ISSUE: 5
INDEXED IN: Scopus WOS
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TITLE: Precision medicine for rare diseases: The times they are A-Changin'  Full Text
AUTHORS: Amaral, Margarida D.;
PUBLISHED: 2022, SOURCE: CURRENT OPINION IN PHARMACOLOGY, VOLUME: 63
INDEXED IN: Scopus WOS
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