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TITLE: Letter to the editor of JCF  Full Text
AUTHORS: Margarida D Amaral;
PUBLISHED: 2020, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 19, ISSUE: 3
INDEXED IN: Scopus WOS
32
TITLE: Characterization of the mechanism of action of RDR01752, a novel corrector of F508del-CFTR  Full Text
AUTHORS: Miqueias Lopes Pacheco; Iris A L Silva; Mark J Turner; Graeme W Carlile; Elvira Sondo; David Y Thomas; Nicoletta Pedemonte; John W Hanrahan; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: BIOCHEMICAL PHARMACOLOGY, VOLUME: 180
INDEXED IN: Scopus WOS
33
TITLE: KLF4 Acts as a wt-CFTR Suppressor through an AKT-Mediated Pathway  Full Text
AUTHORS: Luis Sousa; Ines Pankonien; Luka A Clarke; Iris Silva; Karl Kunzelmann; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: CELLS, VOLUME: 9, ISSUE: 7
INDEXED IN: Scopus WOS
34
TITLE: Cytoskeleton regulators CAPZA2 and INF2 associate with CFTR to control its plasma membrane levels under EPAC1 activation
AUTHORS: Santos, JD; Pinto, FR; Ferreira, JF; Amaral, MD; Zaccolo, M; Farinha, CM;
PUBLISHED: 2020, SOURCE: The Biochemical journal, VOLUME: 477, ISSUE: 13
INDEXED IN: Scopus
35
TITLE: Organoids as a personalized medicine tool for ultra-rare mutations in cystic fibrosis: The case of S955P and 1717-2A > G  Full Text
AUTHORS: Iris A L Silva; Tereza Dousova; Sofia Ramalho; Raquel Centeio; Luka A Clarke; Violeta Railean; Hugo M Botelho; Andrea Holubova; Iveta Valaskova; Jiunn Tyng Yeh; Tzyh Chang Hwang; Carlos M Farinha; Karl Kunzelmann; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: BIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR BASIS OF DISEASE, VOLUME: 1866, ISSUE: 11
INDEXED IN: Scopus WOS
36
TITLE: Impact of KLF4 on Cell Proliferation and Epithelial Differentiation in the Context of Cystic Fibrosis  Full Text
AUTHORS: Luis Sousa; Ines Pankonien; Filipa B Simoes; Marc Chanson; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 21, ISSUE: 18
INDEXED IN: Scopus WOS
37
TITLE: Mutant CFTR Drives TWIST1 mediated epithelial-mesenchymal transition  Full Text
AUTHORS: Margarida C Quaresma; Ines Pankonien; Luka A Clarke; Luis S Sousa; Iris A L Silva; Violeta Railean; Tereza Dousova; Jonas Fuxe; Margarida D Amaral;
PUBLISHED: 2020, SOURCE: CELL DEATH & DISEASE, VOLUME: 11, ISSUE: 10
INDEXED IN: Scopus WOS
38
TITLE: Assessment of Distinct Electrophysiological Parameters in Rectal Biopsies for the Choice of the Best Diagnosis/Prognosis Biomarkers for Cystic Fibrosis  Full Text
AUTHORS: Silva, IAL; Duarte, A; Marson, FAL; Centeio, R; Dousova, T; Kunzelmann, K; Amaral, MD;
PUBLISHED: 2020, SOURCE: FRONTIERS IN PHYSIOLOGY, VOLUME: 11
INDEXED IN: Scopus WOS
39
TITLE: An open-source high-content analysis workflow for CFTR function measurements using the forskolin-induced swelling assay  Full Text
AUTHORS: Hagemeijer, MC; Vonk, AM; Awatade, NT; Silva, IAL; Tischer, C; Hilsenstein, V; Beekman, JM; Amaral, MD; Botelho, HM;
PUBLISHED: 2020, SOURCE: BIOINFORMATICS, VOLUME: 36, ISSUE: 24
INDEXED IN: Scopus WOS
40
TITLE: R560S: A class II CFTR mutation that is not rescued by current modulators  Full Text
AUTHORS: Nikhil T Awatade; Sofia Ramalho; Iris A L Silva; Vernica Felicio; Hugo M Botelho; Eyleen de Poel; Annelotte Vonk; Jeffrey M Beekman; Carlos M Farinha; Margarida D Amaral;
PUBLISHED: 2019, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 18, ISSUE: 2
INDEXED IN: Scopus WOS
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